Urea Cycle Disorders Market Growth to Accelerate in Forecast Period (2023-2032), DelveInsight Analyzes | Aeglea BioTherapeutics, Ultragenyx Pharmaceutical, Arcturus Therapeutics, Horizon Pharma

DelveInsight's "Urea Cycle Disorders Market Insights, Epidemiology, and Market Forecast-2032″ report offers an in-depth understanding of the Urea Cycle Disorders, historical and forecasted epidemiology as well as the Urea Cycle Disorders market trends in the United States, EU4 (Germany, Spain, Italy, France) the United Kingdom and Japan.

To Know in detail about the Urea Cycle Disorders market outlook, drug uptake, treatment scenario and epidemiology trends, Click here; Urea Cycle Disorders Market Forecast
https://www.delveinsight.com/sample-request/urea-cycle-disorders-market?utm_source=openpr&utm_medium=pressrelease&utm_campaign=gpr

Some of the key facts of the Urea Cycle Disorders Market Report:
• The Urea Cycle Disorders market size is anticipated to grow with a significant CAGR during the study period (2019-2032)
• In April 2024, iECURE has obtained approval for its Investigational New Drug (IND) application from the United States Food and Drug Administration (US FDA) for ECUR-506 in ornithine transcarbamylase (OTC) deficiency.
• In March 2024, CAMP4 Therapeutics Corp., a clinical-stage biotechnology firm utilizing regulatory RNA to restore healthy gene expression, announced today that the initial participant has been dosed in its Phase 1 clinical trial of CMP-CPS-001, a potential first-in-class treatment for urea cycle disorders (UCDs).
• In December 2023, The European Commission approved LOARGYS (pegzilarginase) for treating arginase 1 deficiency (ARG1-D) in adults, adolescents, and children aged 2 years and older. Shortly afterward, the company expressed plans to resubmit the Biologics License Application (BLA) in the US in 2024, seeking approval for LOARGYS in the treatment of ARG1-D.
• According to Centers for Disease Control and Prevention reports from 2022, it is estimated that urea cycle disorders (UCD) occur in approximately 1 in 8,500 births. Research indicates that a significant number of UCD cases remain undiagnosed, and tragically, some affected newborns pass away without receiving a definitive diagnosis.
• Stone et al. (2023) reported that approximately 66% of urea cycle disorders (UCDs) are caused by mutations in OTC, around 20% by ASS1 mutations, and approximately 10% by ASL mutations.
• Sawada et al. (2022) conducted a study estimating that urea cycle disorders (UCDs) have an incidence ranging from approximately 1 in every 8,000 to 44,000 births. Ornithine transcarbamylase deficiency (OTCD), the most prevalent UCD, is inherited as an X-linked trait.
• Key Urea Cycle Disorders Companies: Acer Therapeutics, Dimension Therapeutics, Callitas Therapeutics, Poseida Therapeutics, Promethera Biosciences, Arcturus Therapeutics, Kaleido Biosciences, Akaza Biopharma, Evox Therapeutics, Dipharma SA, Sana Biotechnology, Aeglea BioTherapeutics, Erytech, and others
• Key Urea Cycle Disorders Therapies: LUNAR-OTC (ARCT-810), ECUR-506, AEB1102 (pegzilarginase), DTX301, ARCT-810, HPN-100, RAVICTI, and others
• The Urea Cycle Disorders epidemiology based on gender analyzed that OTC deficiency affects males more often than females and most males are symptomatic in nature. In males, symptoms typically begin during the first few days of life
• The Urea Cycle Disorders market is expected to surge due to the disease's increasing prevalence and awareness during the forecast period. Furthermore, launching various multiple-stage Urea Cycle Disorders pipeline products will significantly revolutionize the Urea Cycle Disorders market dynamics.

Urea Cycle Disorders Overview
Urea Cycle Disorders (UCDs) are a group of inherited metabolic disorders that affect the body's ability to remove ammonia from the blood. Ammonia is a waste product produced when proteins are broken down in the body. Normally, the liver converts ammonia into urea, which is then eliminated from the body through urine. In individuals with UCDs, this process is impaired due to deficiencies in enzymes that are necessary for the urea cycle.

Get a Free sample for the Urea Cycle Disorders Market Report:
https://www.delveinsight.com/report-store/urea-cycle-disorders-market?utm_source=openpr&utm_medium=pressrelease&utm_campaign=gpr

Urea Cycle Disorders Epidemiology
The epidemiology section provides insights into the historical, current, and forecasted epidemiology trends in the seven major countries (7MM) from 2019 to 2032. It helps to recognize the causes of current and forecasted trends by exploring numerous studies and views of key opinion leaders. The epidemiology section also provides a detailed analysis of the diagnosed patient pool and future trends.

Urea Cycle Disorders Epidemiology Segmentation:
The Urea Cycle Disorders market report proffers epidemiological analysis for the study period 2019-2032 in the 7MM segmented into:
• Total Incident Cases of Urea Cycle Disorders in the 7MM
• Onset-specific Cases of Urea Cycle Disorders in the 7MM
• Type-specific Cases of Urea Cycle Disorders in the 7MM
• Diagnosed and Treatable Cases of Urea Cycle Disorders in the 7MM

Download the report to understand which factors are driving Urea Cycle Disorders epidemiology trends @ Urea Cycle Disorders Epidemiology Forecast
https://www.delveinsight.com/sample-request/urea-cycle-disorders-market?utm_source=openpr&utm_medium=pressrelease&utm_campaign=gpr

Urea Cycle Disorders Drugs Uptake and Pipeline Development Activities
The drugs uptake section focuses on the rate of uptake of the potential drugs recently launched in the Urea Cycle Disorders market or expected to get launched during the study period. The analysis covers Urea Cycle Disorders market uptake by drugs, patient uptake by therapies, and sales of each drug.
Moreover, the therapeutics assessment section helps understand the drugs with the most rapid uptake and the reasons behind the maximal use of the drugs. Additionally, it compares the drugs based on market share.
The report also covers the Urea Cycle Disorders Pipeline Development Activities. It provides valuable insights about different therapeutic candidates in various stages and the key companies involved in developing targeted therapeutics. It also analyzes recent developments such as collaborations, acquisitions, mergers, licensing patent details, and other information for emerging therapies.

Urea Cycle Disorders Therapies and Key Companies
• LUNAR-OTC (ARCT-810): Arcturus Therapeutics
• ECUR-506: iECURE
• AEB1102 (pegzilarginase): Aeglea BioTherapeutics
• DTX301: Ultragenyx Pharmaceutical
• ARCT-810: Arcturus Therapeutics
• HPN-100: Horizon Pharma
• RAVICTI: Horizon Therapeutics, LLC

Discover more about therapies set to grab major Urea Cycle Disorders market share @ Urea Cycle Disorders Treatment Market
https://www.delveinsight.com/sample-request/urea-cycle-disorders-market?utm_source=openpr&utm_medium=pressrelease&utm_campaign=gpr

Urea Cycle Disorders Market Strengths
• Initial signs of translational promise in early phase clinical trials in late-onset OTCdeficient adult patients are paving the way for a wider development of gene therapy for younger patients and for all UCDs.
• LOARGYS (pegzilarginase), approved in Europe, is the first and only disease modifying treatment for ARG1-D.

Urea Cycle Disorders Market Opportunities
• UCDs emerging landscape consist of various gene therapies and mRNA therapies that have the potential to address the genetic deficiencies responsible for UCDs, potentially minimizing the need for nitro scavengers by intervening earlier in the urea cycle.
• A better understanding of UCDs genotypes may allow for more personalized treatment plans based on the specific genetic mutations involved.

Scope of the Urea Cycle Disorders Market Report
• Study Period: 2019-2032
• Coverage: 7MM [The United States, EU5 (Germany, France, Italy, Spain, and the United Kingdom), and Japan]
• Key Urea Cycle Disorders Companies: Acer Therapeutics, Dimension Therapeutics, Callitas Therapeutics, Poseida Therapeutics, Promethera Biosciences, Arcturus Therapeutics, Kaleido Biosciences, Akaza Biopharma, Evox Therapeutics, Dipharma SA, Sana Biotechnology, Aeglea BioTherapeutics, Erytech, and others
• Key Urea Cycle Disorders Therapies: LUNAR-OTC (ARCT-810), ECUR-506, AEB1102 (pegzilarginase), DTX301, ARCT-810, HPN-100, RAVICTI, and others
• Urea Cycle Disorders Therapeutic Assessment: Urea Cycle Disorders current marketed and Urea Cycle Disorders emerging therapies
• Urea Cycle Disorders Market Dynamics: Urea Cycle Disorders market drivers and Urea Cycle Disorders market barriers
• Competitive Intelligence Analysis: SWOT analysis, PESTLE analysis, Porter's five forces, BCG Matrix, Market entry strategies
• Urea Cycle Disorders Unmet Needs, KOL's views, Analyst's views, Urea Cycle Disorders Market Access and Reimbursement

To know more about Urea Cycle Disorders companies working in the treatment market, visit @ Urea Cycle Disorders Clinical Trials and Therapeutic Assessment
https://www.delveinsight.com/sample-request/urea-cycle-disorders-market?utm_source=openpr&utm_medium=pressrelease&utm_campaign=gpr

Table of Contents
1. Urea Cycle Disorders Market Report Introduction
2. Executive Summary for Urea Cycle Disorders
3. SWOT analysis of Urea Cycle Disorders
4. Urea Cycle Disorders Patient Share (%) Overview at a Glance
5. Urea Cycle Disorders Market Overview at a Glance
6. Urea Cycle Disorders Disease Background and Overview
7. Urea Cycle Disorders Epidemiology and Patient Population
8. Country-Specific Patient Population of Urea Cycle Disorders
9. Urea Cycle Disorders Current Treatment and Medical Practices
10. Urea Cycle Disorders Unmet Needs
11. Urea Cycle Disorders Emerging Therapies
12. Urea Cycle Disorders Market Outlook
13. Country-Wise Urea Cycle Disorders Market Analysis (2019-2032)
14. Urea Cycle Disorders Market Access and Reimbursement of Therapies
15. Urea Cycle Disorders Market Drivers
16. Urea Cycle Disorders Market Barriers
17. Urea Cycle Disorders Appendix
18. Urea Cycle Disorders Report Methodology
19. DelveInsight Capabilities
20. Disclaimer
21. About DelveInsight

Latest Reports by DelveInsight

Listeriosis Market
https://www.delveinsight.com/report-store/listeriosis-market
DelveInsight's comprehensive report titled "Listeriosis Market Insights, Epidemiology, and Market Forecast - 2034" offers a detailed analysis of Listeriosis. The report presents historical and projected epidemiological data covering incident cases of listeriosis, age-specific cases of listeriosis, gender-specific cases of listeriosis, risk-associated cases of listeriosis, and treated cases of listeriosis.

Dysfunctional Uterine Bleeding Market
https://www.delveinsight.com/report-store/dysfunctional-uterine-bleeding-market
DelveInsight's "Dysfunctional Uterine Bleeding Market Insights, Epidemiology, and Market Forecast-2032" report delivers an in-depth understanding of the Dysfunctional Uterine Bleeding, historical and forecasted epidemiology as well as the Dysfunctional Uterine Bleeding market trends in the United States, EU5 (Germany, Spain, Italy, France, and United Kingdom) and Japan.

Mrna Based Vaccines And Therapeutics Market
https://www.delveinsight.com/report-store/global-messenger-rna-mrna-based-vaccines-and-therapeutics-market
DelveInsight's "Global Messenger RNA (mRNA)-based Vaccines and Therapeutics- Market Insights, Epidemiology, and Market Forecast-2032" report delivers an in-depth understanding of the Global Messenger RNA (mRNA)-based Vaccines and Therapeutics, historical and forecasted epidemiology as well as the Global Messenger RNA (mRNA)-based Vaccines and Therapeutics market trends in the United States, EU5 (Germany, Spain, Italy, France, and United Kingdom) and Japan.

Papilloma Market
https://www.delveinsight.com/report-store/papilloma-market
DelveInsight's "Papilloma Market Insights, Epidemiology, and Market Forecast-2032" report delivers an in-depth understanding of the Papilloma, historical and forecasted epidemiology as well as the Papilloma market trends in the United States, EU5 (Germany, Spain, Italy, France, and United Kingdom) and Japan.

Periodontal Disease Market
https://www.delveinsight.com/report-store/periodontal-disease-market
DelveInsight's "Periodontal Disease Market Insights, Epidemiology, and Market Forecast-2032" report delivers an in-depth understanding of the Periodontal Disease, historical and forecasted epidemiology as well as the Periodontal Disease market trends in the United States, EU5 (Germany, Spain, Italy, France, and the United Kingdom) and Japan.

Media Contact
Company Name: DelveInsight Business Research LLP
Contact Person: Gaurav Bora
Email: info@delveinsight.com
City: Albany
State: New York
Country: United States
Website: https://www.delveinsight.com/consulting

About DelveInsight
DelveInsight is a leading Healthcare Business Consultant, and Market Research firm focused exclusively on life sciences. It supports Pharma companies by providing comprehensive end-to-end solutions to improve their performance.
It also offers Healthcare Consulting Services, which benefits in market analysis to accelerate the business growth and overcome challenges with a practical approach.

This release was published on openPR.