openPR Logo
Press release

Global Gaucher Disease Treatment Market

03-27-2017 02:11 PM CET | Health & Medicine

Press release from: Persistence Market Research Pvt. Ltd

Gaucher disease is recessive gene dominance disorder with massive clinical heterogeneity. Symptoms of the disease include painless splenomegaly, anemia, or thrombocytopenia, chronic fatigue, hepatomegaly, bone pain, and pathologic fractures. The disease also contributes to easy incidence of bruising and bleeding through the nose. Manifested in three sub-types, the disease results from the deficiency of the enzyme glucocerebrosidase. It is the most common lysosomal storage disorder and has an incidence of approximately 1 for every 50,000 live births. The most severe form of the disease is the perinatal lethal form. Gaucher disease is said to exhibit the highest manifestation in Jewish population of Eastern and Central European region, affecting 1 out of every 450 people and the number of disease carriers is 1 out of every 10 within the descent. Increasing medical advancement in research and development for rare disorders is leading to rising awareness and could eventually lead to a cure for such rare disorders.

In past, recombinant enzyme imiglucerase was used in most patients. The treatment was effective in retrograding the visceral and hematologic symptoms of Gaucher disease. However, slow responses of the skeletal disease and pulmonary involvement is comparatively resistant to the enzyme. Treatment for Gaucher disease is typically given in high dose once a week, but, in some cases, medium dose of medicine is given every week or three times in low dose quantity. Significant responses have been observed in all type of dose regimens.

The lack of drugs in last stage of development is anticipated to limit the expansion of the Gaucher disease market, although the rise in number of patient globally tend to favor the growth of Gaucher disease treatment in the market over the forecast period. Furthermore, ERT is suggested for patients with type 1 Gaucher disease exhibiting the sign and symptoms such as anemia, thrombocytopenia and bone disorder. However, sternness and progression rate of disease varies, mainly in adults, which complicates the treatment decision for the medical specialist. Enzyme replacement therapy has widely improved the quality of life for the patients. Companies involved in producing the enzyme has also gained traction in the profit margins. As a result, the major players in this industries are strictly working for the development of the latest drug therapy for the patients suffering from Gaucher disease. Since, the population suffering from Gaucher disease is comparatively less than other fatal diseases, the treatment is costlier and development is slow. Unfortunately, it has been anticipated that in spite of improvements in diagnosis and treatment, major chunk of population having Gaucher disease may not be treated over the forecast period, due to late or misdiagnosis of the Gaucher disease, which will further affect the market.

Increased focus on formation of research consortiums on rare diseases is leading to rising disease awareness levels and increased reporting of such diseases too. Furthermore, rising affordability for access to essential healthcare services is contributing largely to disease testing and identification at early stages. Availability of symptomatic control options and validation of the same in international consortiums and federations has been leading to greater availability of symptom control options.

Barriers include lack of companies researching on cures due to profitability issues of targeted therapy. Lack of awareness among physicians also contributes largely towards no treatments or wrong treatments. Also professional counselling is one of the most effective mediums of disease management, stigmatization of patient leads to psychological issues thus leading to absence of proper treatments.

On the basis of region presence, Gaucher disease treatment market is segmented into five key regions: North America, Latin America, Europe, Asia Pacific, and Middle East & Africa. Presently, North America dominates the global market for Gaucher disease treatment market due to high diagnose rate and large number of facilities for enzyme replacement therapy. However, growth in Middle East and African region is expected to take exponential growth in terms of CAGR over the forecast period. Rising number of people with bone disorder is expected to fuel the Gaucher disease treatment market. The U.S. Gaucher disease treatment market is expected to dominate in terms of market share with major share among all the regions.

A Sample of this Report is Available Upon Request @

Some of the major market players in Gaucher disease treatment market globally includes, Abbott , Aptalis Pharma , Genzyme Corporation, GlaxoSmithKline (GSK), Pfizer Inc., Shire Human Genetic Therapies, Inc., Eli Lilly and Company, Enobia Pharma Inc., Anthera Pharmaceuticals, Inc., BioMarin Pharmaceutical Inc., MedPro Rx, Zymenex A/S, Merck Serono.

Request to View Tables of Content @

About Us
Persistence Market Research (PMR) is a U.S.-based full-service market intelligence firm specializing in syndicated re-search, custom research, and consulting services. PMR boasts market research expertise across the Healthcare, Chemicals and Materials, Technology and Media, Energy and Mining, Food and Beverages, Semiconductor and Electronics, Con-sumer Goods, and Shipping and Transportation industries. The company draws from its multi-disciplinary capabilities and high-pedigree team of analysts to share data that precisely corresponds to clients’ business needs.
PMR stands committed to bringing more accuracy and speed to clients’ business decisions. From ready-to-purchase market research reports to customized research solutions, PMR’s en-gagement models are highly flexible without compromising on its deep-seated research values.

Persistence Market Research Pvt. Ltd
305 Broadway
7th Floor, New York City,
NY 10007, United States,
USA – Canada Toll Free: 800-961-0353

This release was published on openPR.

Permanent link to this press release:

Please set a link in the press area of your homepage to this press release on openPR. openPR disclaims liability for any content contained in this release.

You can edit or delete your press release Global Gaucher Disease Treatment Market here

News-ID: 483026 • Views: 681

More Releases from Persistence Market Research Pvt. Ltd

Global HPMC Capsules Market is expected to reach a Valuation of US$ 554.5 Mn Ove …
HPMC capsules are strictly non-toxic and qualify to be Kosher and Halal-certified, which is why their popularity has grown in several parts of the world. Moreover, these capsules can significantly boost the body metabolism by improving absorption and digestion of protein, fat and carbohydrates. HPMC capsules find their application in the preparation of non-animal based medicines and cosmetics & nutraceuticals products. Persistence Market Research (PMR) recently conducted a study
Vacuum Tissue Processor Technology Most Favored in the Global Tissue Processing …
Persistence Market Research has come up with a fact based analytical research study describing various aspects of the tissue processing systems market across the globe. The analysis on tissue processing systems has been systematically drafted in a new research publication titled “Tissue Processing Systems Market: Global Industry Analysis (2012-2016) and Forecast (2017-2025)”. This comprehensive research report focuses on various developments, trends, restraints, opportunities, drivers and challenges impacting revenue growth of
Endodontics Market Is Projected To Grow At A Moderate CAGR During The Period Of …
Endodontics is associated with the dentistry segment. It involves several therapies to protect the human teeth from infections and injuries caused to the dental pulp. Generally, it is concerned with morphology, pathology as well as physiology of dental pulp and the periradicular tissues. Endodontics is important during carrying out root canal procedure in order to reduce the inflammation and to end infection. Modernization has touched the field of endodontics as
Global Home Infusion Therapy Devices Market Driven by Growing Incidence of Pain, …
According to the latest market report published by Persistence Market Research titled ‘Home Infusion Therapy Devices Market: Global Industry Analysis (2012-2016) and Forecast (2017-2025),’ the global Home Infusion Therapy Devices market is expected to expand at a CAGR of 6.8% during the forecast period 2017–2025. Persistence Market Research delivers key insights and presents a revised forecast of the global Home Infusion Therapy Devices market for an eight year period from

All 5 Releases

More Releases for Gaucher

Gaucher Disease Market Development Trends, Competitive Landscape and Key Regions
Gaucher Disease Market is a Professional and in-depth market research on the current state of the Global Gaucher Disease. The report provides a basic overview of the industry including definitions, classifications, applications and industry chain structure. The Gaucher Disease Market analysis is provided for the international market including development history, competitive landscape analysis, and by major regions development status (Asia-Pacific, North America, Europe, Middle East & Africa), and other regions
Gaucher Disease Market Pharmaceuticals & Healthcare Analysis 2018 to 2025
In 2017, the global Gaucher Disease market size was million US$ and it is expected to reach million US$ by the end of 2025, with a CAGR of during 2018-2025. Companies Mentioned are: Sanofi, Shire, Actelion Pharma, Pfizer, ISU Pharm, .... Sample/Inquiry at: Further, the market is segmented based on the applications, types and Geography area such as  Gaucher Disease Market, by Types: Enzyme Replacement Therapy Substrate Reduction Therapy Gaucher Disease Market, by Applications: Non-Neuronopathic Gaucher Disease Neuronopathic Gaucher Disease Geographically,
Gaucher Disease Treatment Market, by Disease Type, Therapy Type
Gaucher disease is an autosomal recessive inherited metabolism disorder where a type of fat (lipid) called glucocerebroside is unable to degrade. Body synthesis enzyme called glucocerebrosidase, which breakdowns and reprocesses glucocerebroside. Gaucher disease is caused by mutations of a single gene called GBA, which leads to very low levels of glucocerebrosidase enzyme leading to low degradation of glucocerebroside. There are three types of Gaucher disease namely: type 1, type 2,
Global Gaucher Disease Market Trends, Analysis, Players & Forecast by 2025
An up-to-date research report has been disclosed by Market Research Hub highlighting the title “Global Gaucher Disease Market Research Report 2018” which provides an outlook of current market growth as well as the expected forecast including Rate on Investment (ROI) together with growing CAGR near XX% during 2018-2025. The report studies gate drivers in global market, especially in North America, China, Europe, Southeast Asia, Japan and India, with production, revenue,
United States Gaucher Disease Market Report 2017
In this report, the United States Gaucher Disease market is valued at USD XX million in 2016 and is expected to reach USD XX million by the end of 2022, growing at a CAGR of XX% between 2016 and 2022. Geographically, this report splits the United States market into seven regions: The West Southwest The Middle Atlantic New England The South The Midwest with sales (volume), revenue (value), market share and growth rate of Gaucher Disease in these
Gaucher Disease Market 2017 - Sanofi, Shire, Actelion Pharma, Pfizer
Apex Research, recently published a detailed market research study focused on the "Gaucher Disease Market" across the global, regional and country level. The report provides 360° analysis of "Gaucher Disease Market" from view of manufacturers, regions, product types and end industries. The research report analyses and provides the historical data along with current performance of the global Gaucher Disease industry, and estimates the future trend of Gaucher Disease market on