Hemophilia A Pipeline Drugs Insights Report 2025: Emerging Therapeutics and Market Opportunities Revealed | DelveInsight

DelveInsight's "Hemophilia A Pipeline Insights 2025" report provides comprehensive insights about 40+ companies and 40+ pipeline drugs in the Hemophilia A pipeline landscape. It covers the Hemophilia A pipeline drug profiles, including clinical and nonclinical stage products. It also covers the Hemophilia A pipeline therapeutics assessment by product type, stage, route of administration, and molecule type. It further highlights the inactive pipeline products in this space.

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Key Takeaways from the Hemophilia A Pipeline Report
• On 10 October 2025, Hoffmann-La Roche conducted a Phase I/II Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of NXT007 in Persons With Severe or Moderate Hemophilia A.
• On 08 October 2025, BioMarin Pharmaceutical announced a Phase III clinical study will evaluate the safety and effectiveness of valoctocogene roxaparvovec in combination with prophylactic corticosteroids in patients with severe hemophilia A.
• DelveInsight's Hemophilia A pipeline report depicts a robust space with 40+ active players working to develop 40+ pipeline therapies for Hemophilia A treatment.
• The leading Hemophilia A Companies such as Hoffmann-La Roche, Chugai Pharmaceutical, Shire, Pfizer, BioMarin Pharmaceutical, Sinocelltech Ltd., Bayer, Ultragenyx Pharmaceutical, Spark Therapeutics, Octapharma, ApcinteX Ltd., Chia Tai Tianqing Pharmaceutical Group Co., Ltd., Expression Therapeutics, LLC, CSL Behring and others.
• Promising Hemophilia A Pipeline Therapies such as Emicizumab, rFVIIa, aPCC, BAX 888, OBIZUR, BIIB031 (rFVIIIFc), Recombinant Human Coagulation FVIII, and others.

Stay ahead with the most recent pipeline outlook for Hemophilia A. Get insights into clinical trials, emerging therapies, and leading companies with DelveInsight @ Hemophilia A Treatment Drugs- https://www.delveinsight.com/sample-request/hemophilia-a-pipeline-insight-2020?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Hemophilia A Emerging Drugs Profile
• AGN-193408: Allergan
Allergan is conducting a multicenter, open-label, dose escalation (Cohort 1) to masked, randomized, parallel-group (Cohort 2) study to evaluate the safety and efficacy of AGN-193408 SR in participants with open-angle glaucoma or ocular hypertension. It is an implant containing preservative-free AGN-193408 dispersed in a biodegradable polymer matrix.

• OCTA101: Octapharma
Octapharma is evaluating OCTA101 (a human-cl rhFVIII and recombinant human von Willebrand Factor fragment dimer) under a Phase 1/2 study, which will be a dose escalation study in adults in 5 cohorts, with the main purpose to assess the safety of subcutaneous injection of OCTA101 (in previously treated adult patients with severe hemophilia A. The study also aims to assess the pharmacokinetics (PK) characteristics, dose proportionality, and subcutaneous bioavailability of OCTA101 compared with intravenous administration of Nuwiq (Human-cl rh FVIII), in order to define the prophylactic treatment (dose and injection interval) that would result in protective trough levels of FVIII:C for future Phase 3 studies. By Data Monitoring Committee recommendation, patients enrolled in cohorts 1, 2 and 3 will proceed to 3-month prophylactic treatment to receive daily dosing of OCTA101 for 3 months.

• Valoctocogene roxaparvovec: BioMarin Pharmaceuticals
Valoctocogene roxaparvovec, is an investigational gene therapy in clinical trials for the treatment of Hemophilia A and has not been determined to be safe or effective. Valoctocogene roxaparvovec is administered as a single infusion. The ongoing clinical trials will determine if the new gene will enable the body to produce factor VIII. Following infusion, clinical trial subjects are being evaluated to determine the safety profile, changes in Factor VIII activity levels, changes in factor replacement usage, changes in reported bleeds requiring factor replacement, and quality of life measures, among other endpoints.

The Hemophilia A Pipeline Report Provides Insights into
• The report provides detailed insights about companies that are developing therapies for the treatment of Hemophilia A with aggregate therapies developed by each company for the same.
• It accesses the Different therapeutic candidates segmented into early-stage, mid-stage, and late-stage of development for Hemophilia A Treatment.
• Hemophilia A Companies are involved in targeted therapeutics development with respective active and inactive (dormant or discontinued) projects.
• Hemophilia A Drugs under development based on the stage of development, route of administration, target receptor, monotherapy or combination therapy, a different mechanism of action, and molecular type.
• Detailed analysis of collaborations (company-company collaborations and company-academia collaborations), licensing agreement and financing details for future advancement of the Hemophilia A market

Explore groundbreaking therapies and clinical trials in the Hemophilia A Pipeline. Access DelveInsight's detailed report now! @ New Hemophilia A Drugs- https://www.delveinsight.com/sample-request/hemophilia-a-pipeline-insight-2020?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Hemophilia A Companies
Hoffmann-La Roche, Chugai Pharmaceutical, Shire, Pfizer, BioMarin Pharmaceutical, Sinocelltech Ltd., Bayer, Ultragenyx Pharmaceutical, Spark Therapeutics, Octapharma, ApcinteX Ltd., Chia Tai Tianqing Pharmaceutical Group Co., Ltd., Expression Therapeutics, LLC, CSL Behring and others.

Hemophilia A pipeline report provides the therapeutic assessment of the pipeline drugs by the Route of Administration. Products have been categorized under various ROAs such as
• Oral
• Intravenous
• Subcutaneous
• Molecule Type

Hemophilia A Products have been categorized under various Molecule types such as
• Small molecules
• Gene Therapies
• Bispecific antibodies
• Recombinant proteins
• Fusion Proteins
• Coagulants
• Blood coagulation factor replacements

Unveil the future of Hemophilia A Treatment. Learn about new drugs, pipeline developments, and key companies with DelveInsight's expert analysis @ Hemophilia A Market Drivers and Barriers- https://www.delveinsight.com/sample-request/hemophilia-a-pipeline-insight-2020?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Scope of the Hemophilia A Pipeline Report
• Coverage- Global
• Hemophilia A Companies- Hoffmann-La Roche, Chugai Pharmaceutical, Shire, Pfizer, BioMarin Pharmaceutical, Sinocelltech Ltd., Bayer, Ultragenyx Pharmaceutical, Spark Therapeutics, Octapharma, ApcinteX Ltd., Chia Tai Tianqing Pharmaceutical Group Co., Ltd., Expression Therapeutics, LLC, CSL Behring and others.
• Hemophilia A Pipeline Therapies- Emicizumab, rFVIIa, aPCC, BAX 888, OBIZUR, BIIB031 (rFVIIIFc), Recombinant Human Coagulation FVIII, and others.
• Hemophilia A Therapeutic Assessment by Product Type: Mono, Combination, Mono/Combination
• Hemophilia A Therapeutic Assessment by Clinical Stages: Discovery, Pre-clinical, Phase I, Phase II, Phase III

Get the latest on Hemophilia A Therapies and clinical trials. Download DelveInsight's in-depth pipeline report today! @ Hemophilia A Companies, Key Products and Unmet Needs- https://www.delveinsight.com/sample-request/hemophilia-a-pipeline-insight-2020?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Table of Contents
1. Introduction
2. Executive Summary
3. Hemophilia A: Overview
4. Pipeline Therapeutics
5. Therapeutic Assessment
6. Hemophilia A - DelveInsight's Analytical Perspective
7. In-depth Commercial Assessment
8. Hemophilia A Collaboration Deals
9. Late Stage Products (Pre-registration)
10. Valoctocogene roxaparvovec: BioMarin Pharmaceutical
11. Late Stage Products (Phase III)
12. Giroctocogene fitelparvovec: Pfizer/ Sangamo Therapeutics
13. Mid Stage Products (Phase II)
14. Comparative Analysis
15. NNC0365-3769 A (Mim8): Novo Nordisk A/S
16. Early Stage Products (Phase I/II)
17. Comparative Analysis
18. BAX 888: Baxalta / Shire
19. BAY2599023: Bayer / Ultragenix pharmaceutical
20. Early Stage Products (Phase I)
21. Gene therapy: Expression Therapeutics, LLC
22. Hemophilia A Key Companies
23. Hemophilia A Key Products
24. Hemophilia A- Unmet Needs
25. Hemophilia A- Market Drivers and Barriers
26. Hemophilia A- Future Perspectives and Conclusion
27. Hemophilia A Analyst Views
28. Hemophilia A Key Companies
29. Appendix

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