openPR Logo
Press release

Upcoming Event on 'Orphan Drugs and Rare Diseases Conference - US Edition' | 17th - 18th October 2024 | Boston, USA

06-20-2024 01:32 PM CET | Health & Medicine

Press release from: MNMConferences

Upcoming Event on 'Orphan Drugs and Rare Diseases Conference - US

Join us at our MarketsandMarkets Orphan Drugs and Rare Diseases Conference in Boston, USA for a groundbreaking exploration of the recent advances in developing life-saving therapies, technologies in diagnosing, and strategies to enhance orphan drug development.

The conference will focus on the wide scope of orphan drug developments, critical issues of elevated pricing, reimbursement & access to patients, and strategies to enhance access to novel diagnostics and effective therapies for rare to ultra-rare diseases.

Register Now @ https://events.marketsandmarkets.com/orphan-drugs-and-rare-diseases-conference-us-edition/register

Conference Speakers-

1. Joslyn Arnon Crowe- Executive Director, National Niemann-Pick Disease Foundation

2. Donna (McKenna) Sullivan- Director of Patient Advocacy, Pathways To Trust

3. Zia Choudhry- Senior Medical Director Rare Autoantibody Diseases - Immunology, Johnson & Johnson

4. Adrian Kielhorn- Senior Director, Global HEOR Neurology, Alexion Pharmaceuticals, Inc

5. Karlie Sharma- Program Director, National Center for Advancing Translational Sciences, National Institutes of Health (NIH/NCATS)

……………. More

Become a speaker @ https://events.marketsandmarkets.com/orphan-drugs-and-rare-diseases-conference-us-edition/speaker-enquiry

Key Sessions-

• Overview and Regulatory Updates: Current Landscape and Regulatory Developments in US Market.

• Emerging Therapies for RDs: Recent breakthroughs in CRISPR-Cas9 technology, Cell & Gene Therapies, mRNA therapies & Precision Treatments.

• Rare Disease and Genetics: Rare Genetic Disease Mechanisms and Therapeutic Targets.

• Patient Advocacy, Engagement & Collaboration: Critical Role of Patient Advocacy and Global Collaboration in Research and Development.

• Global Perspectives and Market Access: Global market dynamics and market access strategies, sustainable models & roadblocks for orphan drugs.

• ……more

Become a Sponsor @ https://events.marketsandmarkets.com/orphan-drugs-and-rare-diseases-conference-us-edition/become-sponsor

ADDRESS:
Magarpatta City, Hadapsar, Pune, India - 411013

About Us-
MarketsandMarkets Conferences, a leading international event organizer since 2014, takes pride in organizing over 200 conferences globally. With our extensive experience and rich legacy, we bring together experts from around the world to drive knowledge sharing and innovation in the healthcare and lifesciences sectors.

This release was published on openPR.

Permanent link to this press release:

Copy
Please set a link in the press area of your homepage to this press release on openPR. openPR disclaims liability for any content contained in this release.

You can edit or delete your press release Upcoming Event on 'Orphan Drugs and Rare Diseases Conference - US Edition' | 17th - 18th October 2024 | Boston, USA here

News-ID: 3546797 • Views:

More Releases from MNMConferences

Upcoming Conference on ImmunoBio Series | 14th - 15th October 2024 | Freiburg, Germany
Upcoming Conference on ImmunoBio Series | 14th - 15th October 2024 | Freiburg, G …
Introducing the 2nd Annual MarketsandMarkets ImmunoBio Series, a groundbreaking event uniting the realms of Biomarker and Immuno-Oncology, set to unfold on 14th - 15th October 2024 in Freiburg, Germany. Register Now @ https://events.marketsandmarkets.com/immunobio-series/register Dive deep into the convergence of biomarkers and immuno-oncology at our flagship conference, where industry pioneers, thought leaders, and experts converge to drive innovation in healthcare and biotechnology. This transformative event offers a dynamic platform for collaboration, knowledge
Upcoming Conference on ImmunoBio Series | 14th - 15th October 2024 | Freiburg im Breisgau, Germany
Upcoming Conference on ImmunoBio Series | 14th - 15th October 2024 | Freiburg im …
Introducing the 2nd Annual MarketsandMarkets ImmunoBio Series, a groundbreaking event uniting the realms of Biomarker and Immuno-Oncology, set to unfold on 14th - 15th October 2024 in Freiburg im Breisgau, Germany. Dive deep into the convergence of biomarkers and immuno-oncology at our flagship conference, where industry pioneers, thought leaders, and experts converge to drive innovation in healthcare and biotechnology. This transformative event offers a dynamic platform for collaboration, knowledge exchange, and
MarketsandMarkets Probiotics Conference | 24th - 25th October 2024 | London, UK
MarketsandMarkets Probiotics Conference | 24th - 25th October 2024 | London, UK
The MarketsandMarkets Probiotics Conference invites you to explore the cutting edge of healthcare on October 24th-25th in London, UK. Delve into the complexities of the human microbiome's influence on health and the environment. Discover the latest breakthroughs in microbiome therapies and probiotics, all while tackling challenges such as limited research and regulatory intricacies. Engage with industry experts across various sectors to gain valuable insights into microbial innovation, regulatory pathways, and
Bridging Data to Decisions: Real-World Evidence and Life Science Analytics Explained | 17th - 18th October 2024| Boston, USA
Bridging Data to Decisions: Real-World Evidence and Life Science Analytics Expla …
We are thrilled to welcome you to the 7th Annual Real-World Evidence and Life Science Analytics Conference at Boston 2024, a premier gathering of thought leaders, industry experts, and innovators at the forefront of revolutionizing healthcare through data-driven insights. Set against the backdrop of advancements in real-world evidence, this conference promises an enriching experience for professionals in life sciences, healthcare, and analytics. The 7th Annual Real-World Evidence and Life Science Analytics

All 5 Releases


More Releases for Disease

Protheragen Announces Disease Model Development Services to Enhance Rare Disease …
Protheragen announced the release of its disease model development services provided to enhance rare disease research. With an increasing focus on rare diseases and the need for tailored research models, Protheragen is dedicated to providing cutting-edge solutions to support this important area of medical research. Rare diseases, which affect a small percentage of the population, pose unique challenges for researchers due to their limited understanding and lack of available treatment options.
Biopharmaceutical Fermentation Market 2022 | Growing Morbidity of Genetic Diseas …
According to Precision Business Insights (PBI), the latest report, the biopharmaceutical fermentation market is expected to be valued at USD 10,302.1 million in 2022, growing at a 4.7% CAGR from 2022 to 2028. The growing prevalence of chronic illness, cancer, cardiac diseases, infectious diseases, antibiotic resistance, autoimmune diseases, etc., globally causes the leaning toward biopharmaceutical products, which show promising results in the research studies. Moreover, new findings by the
Global Inflammatory Bowel Disease (IBD) Market Key Players Analysis, Disease Ind …
Global Inflammatory Bowel Disease (IBD) Market, valued at USD 210.5 Billion in the year 2020 has been driven by factors such as the increasing prevalence of Ulcerative Colitis and Crohn’s Disease, advances in medical technology, government support for inflammatory bowel disease treatment research, and the ubiquity of anxiety and depression. Moreover, factors such as the irregular food habits, unhealthy lifestyle of people, increased level of pollution and increase in alcohol
Moyamoya Disease Market - A Scientometric Assessment of Disease During 2018-23
Market Highlight: Moyamoya disease (MMD) is a chronic, cerebrovascular disease characterized by progressive stenosis in the internal carotid artery and an abnormal vascular network at the base of the brain. The stroke is one of the significant symptoms of moyamoya disease, which further leads to paralysis of the face, arms, and legs, loss of speech, and temporary loss of neurologic function of body parts, visual disturbances, headaches, developmental delay, and
Refsum Disease Industry An Overview of A New Disease - 2018
"Refsum Disease" is a genetic disorder which is inherited as an autosomal recessive trait. The condition is characterized by progressive loss of vision (retinitis pigmentosa), failure of muscle coordination (ataxia), degenerative nerve disease (peripheral neuropathy), and dry, rough, scaly skin (ichthyosis). The accumulation of fatty acid (phytanic acid) in blood plasma and tissues is the main cause of refsum disease. This occurs due to malfunction of the enzyme producing gene
Chagas Disease (Infectious Disease) Pipeline Forecast Report, H1, 2017 [MRH]
Market Research Hub's Pharmaceutical and Healthcare latest pipeline guide Chagas Disease - Pipeline Review, H1 2017, provides comprehensive information on the therapeutics under development for Chagas Disease Market (Infectious Disease), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and