Press release
Gene Therapies for Rare Diseases Market: A Catalyst for Innovation in Gene Editing, Viral Vectors, and Personalized Medicine
InsightAce Analytic Pvt. Ltd. announces the release of a market assessment report on the "Global Gene Therapies For Rare Diseases Market- by Product (Zolgensma, Invossa K, Strimvelis, Neovasculgen, Glybera, Luxturna, Zynteglo and Others), Disease Type (Hemophilia, Duchenne Muscular Dystrophy, Achromatopsia, Cystic Fibrosis, Inherited Retinal Dystrophy, Fragile X Syndrome, Friedreich ataxia, Alpha-1 Antitrypsin Deficiency, Paroxysmal Nocturnal Hemoglobinuria, Retinitis Pigmentosa and Others), Trends, Industry Competition Analysis, Revenue and Forecast To 2031."Request for Sample Pages: https://www.insightaceanalytic.com/request-sample/1091
According to the latest research by InsightAce Analytic, the global Gene Therapies For Rare Diseases market is expected to reach US$ 11,441.6 Million by 2031, with a CAGR of 20.0% during a forecast period of 2023-2031.
Gene therapy plays a pivotal role in the management of rare illnesses. Gene therapy, a targeted and specialized treatment for rare disorders, operates through the insertion of repaired genes into the cells of the patient. Genetic factors contribute to approximately 80% of rare disorders. It is believed that gene therapy could significantly transform the management of rare diseases. Gene therapy presents a viable and enduring alternative to conventional treatment options, while also providing the benefit of one-dose therapy for rare disorders. Gene therapy for rare diseases is developed utilizing an extensive array of manufacturing technologies, such as cell suspension, cell potentiation, and plug-and-play production methods for AAV (adeno-associated virus) serotypes.
The increasing prevalence of rare diseases and the consequential impact on healthcare expenditures are driving substantial market growth for gene therapies designed to treat these conditions. The proliferation of gene therapies for uncommon diseases, the development of innovative gene therapies for the treatment of numerous rare diseases, and the expansion of gene therapy pipelines have all contributed to the rapid adoption of gene treatments. The proliferation of healthcare facilities in diverse geographic regions and the improvement of healthcare affordability have contributed to an increase in the volume of individuals seeking medical care. Additionally, during the forecast period, it is anticipated that rapidly developing gene therapy advancements for the treatment of rare disorders will offer substantial potential. Due to the increased focus on research projects and the creation of novel therapeutic medications, the gene therapy market for rare diseases has experienced a considerable growth in value. The increased adoption of efficacious treatments for rare disorders can be attributed to positive government initiatives aimed at increasing awareness of gene therapies.
It is anticipated that North America will make a contribution to the Gene Therapies For Rare Diseases market. Healthcare expenditure increases are driving the expansion of the gene therapy market for rare diseases, thereby stimulating the development of research organizations in this field. Additionally, the expansion of regional governments is exerting an impact on the trajectory of industry growth. Furthermore, the Asia Pacific gene therapies for rare diseases market is anticipated to experience substantial expansion as a result of the nation's burgeoning research in biomedical and regenerative medicine. Support networks and special regulatory authorities established by the Japanese government have expedited the development of novel pharmaceuticals for the treatment of rare diseases.
Major market players operating in the Gene Therapies For Rare Diseases market include
4d Molecular Therapeutics, LLC, Abeona Therapeutics Inc., Advaxis, Adverum Biotech, Aevi Genomic, Applied Genetic Technologies Corporation (AGTC), Alcyone Lifesciences, Allife Medical Science and Technology, Amarna Therapeutics, American Gene Technologies, Amgen, Amicus Therapeutics, Anchiano Therapeutics, AnGes MG, Apic Bio, Armata Pharmaceuticals, Arrowhead, Arthrogen, Asklepios, Astellas, AVROBIO, BCM Families Foundation, Beijing Northland, Benitec, Biogen, BioMarin, Biosidus, bluebird bio, Boryung Group, Brain Neurotherapeuticsy Bio, Celsion Corporation, Chiesi, CRISPR Therapeutics, CSL Behring, Daewoong Pharma, Dicerna, Editas Medicine, Eiger BioPharmaceuticals, Enzo Therapeutics, Esteve, Evox Therapeutics, Expression Therapeutics, Fibrocell, Flexion Therapeutics,, Fortress Biotech, Freeline Therapeutics, Gene Biotherapeutics, Genenta Science, GeneQuine, Genethon, GenSight, Gilead, Gradalis, GSK, Hanugen, Helixmith, Herantis, ID Pharma, Immusoft, Inovio, Intellia Therapeutics, Intrexon, J&J, Juventas, Kolon Life Science, Krystal Biotech, Locana, LogicBio Therapeutics, Lysogene, Medigene, MeiraGTx, Miltenyi Biotec, Molecular Templates, Momotaro-Gene, Neuralgene, Novartis, OncoSec, Orchard Therapeutics, Oxford Biomedica, Pfizer, Prevail Therapeutics, PTC Therapeutics, REGENXBIO, Renova Therapeutics, Reyon Pharmaceutical, Roche, Rocket Pharma, Roivant, Sangamo Therapeutics, Sarepta Therapeutics, Seelos Therapeutics, Solid BioSciences, Sterna Biologicals, Sutura Therapeutics, SynerGene, Takara, Takeda, Talee Bio, Theragene Pharma, Transgene, Ultragenyx, uniQure, VBL Therapeutics, Vertex, Voyager Therapeutics, Xalud, Xenon, and Ziopharm.
Recent collaborations and agreements in the market:
• In August 2019, Gaboxadol was developed, manufactured, and made widely available in the European market by the U.S. company Ovid Therapeutics in collaboration with the Italian company Angelini Pharma to treat Angelman condition, an uncommon hereditary illness.
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Market Segments
Global Gene Therapies For Rare Diseases Market, by Product, 2023-2031 (Value US$ Mn)
• Zolgensma
• Invossa K
• Glybera
• Luxturna
• Zynteglo
• Strimvelis
• Neovasculgen
• Others
Global Gene Therapies For Rare Diseases Market, by Disease Type, 2023-2031 (Value US$ Mn)
• Hemophilia
• Duchenne Muscular Dystrophy
• Achromatopsia
• Friedreich ataxia
• Alpha-1 Antitrypsin Deficiency
• Paroxysmal Nocturnal Hemoglobinuria
• Cystic Fibrosis
• Inherited Retinal Dystrophy
• Fragile X Syndrome
• Retinitis Pigmentosa
• Others
Global Gene Therapies For Rare Diseases Market, by Region, 2023-2031 (Value US$ Mn)
• North America
• Europe
• Asia Pacific
• Latin America
• Middle East & Africa
North America Gene Therapies For Rare Diseases Market, by country, 2023-2031 (Value US$ Mn)
• U.S.
• Canada
Europe Gene Therapies For Rare Diseases Market, by Country, 2023-2031 (Value US$ Mn)
• Germany
• France
• Italy
• Spain
• Russia
• Rest of Europe
Asia Pacific Gene Therapies For Rare Diseases Market, by country, 2023-2031 (Value US$ Mn)
• India
• China
• Japan
• South Korea
• Australia & New Zealand
Latin America Gene Therapies For Rare Diseases Market, by country, 2023-2031 (Value US$ Mn)
• Brazil
• Mexico
• Rest of Latin America
Middle East & Africa Gene Therapies For Rare Diseases Market, by country, 2023-2031 (Value US$ Mn)
• GCC Countries
• South Africa
• Rest of Middle East & Africa
Why should buy this report:
To receive a comprehensive analysis of the prospects for the global Gene Therapies For Rare Diseases market
To receive an industry overview and future trends of the Gene Therapies For Rare Diseases market
To analyze the Gene Therapies For Rare Diseases market drivers and challenges
To get information on the Gene Therapies For Rare Diseases market value (US$ Mn) forecast to 2030
Significant investments, mergers & acquisitions in the Gene Therapies For Rare Diseases market industry
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InsightAce Analytic is a market research and consulting firm that enables clients to make strategic decisions. Our qualitative and quantitative market intelligence solutions inform the need for market and competitive intelligence to expand businesses. We help clients gain competitive advantage by identifying untapped markets, exploring new and competing technologies, segmenting potential markets and repositioning products. Our expertise is in providing syndicated and custom market intelligence reports with an in-depth analysis with key market insights in a timely and cost-effective manner.
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