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Gene And Cell Therapies In Rare Disorders Market and Epidemiology 2032: Treatment Market, Therapies, Companies, FDA Approvals, Epidemiology and Forecast by DelveInsight | Pfizer, Sangamo Therapeutics, Orchard Therapeutics/ SR-Tiget, Novartis, TVAX Biomedi
DelveInsight's "Gene And Cell Therapies In Rare Disorders Market Insights, Epidemiology, and Market Forecast-2032″ report offers an in-depth understanding of the Gene And Cell Therapies In Rare Disorders, historical and forecasted epidemiology as well as the Gene And Cell Therapies In Rare Disorders market trends in the United States, EU4 (Germany, Spain, Italy, France) the United Kingdom and Japan.To Know in detail about the Gene And Cell Therapies In Rare Disorders market outlook, drug uptake, treatment scenario and epidemiology trends, Click here; Gene And Cell Therapies In Rare Disorders Market Forecast
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Some of the key facts of the Gene And Cell Therapies In Rare Disorders Market Report:
• The Gene And Cell Therapies In Rare Disorders market size is anticipated to grow with a significant CAGR during the study period (2019-2032)
• In February 2024, The French Government has granted €4.9m ($5.3m) to Paris-based Vivet Therapeutics for the development of VTX-806, a gene therapy aimed at treating cerebrotendinous xanthomatosis (CTX), a rare condition causing cholesterol accumulation in nerve cells. This funding is part of the France Health Innovation Plan 2023, under the Biotherapies - Bioproduction in Innovative Therapies acceleration strategy.
• The frequency of DMD is roughly 6 per 100,000 people in Europe and North America, according to the Muscular Dystrophy Association (2023)
• For haemophilia A, there are 12 instances per 100,000 US males, and for haemophilia B, there are 3.7 cases per 100,000 US males, according to the Centres for Disease Control and Prevention (2022)
• The Centres for Disease Control and Prevention estimate that 100,000 Americans have sickle cell disease in 2022
• Pompe disease, commonly known as glycogen storage disease type II (GSD II) or acid maltase deficiency (AMD), is a hereditary illness brought on by a lack of the acid alpha-glucosidase (GAA) enzyme, according to Stevens et al. (2022)
• Key Gene And Cell Therapies In Rare Disorders Companies: Pfizer, Sangamo Therapeutics, Orchard Therapeutics/ SR-Tiget, Novartis, TVAX Biomedical, Aivita Biomedical, RHEACELL GmbH & Co, Capricor Therapeutics, and others
• Key Gene And Cell Therapies In Rare Disorders Therapies: Fidanacogene elaparvovec, GiroctocogenE fitelparvovec, OTL-103, OAV101, TVI-Brain-1, AV-GBM-1, ABCB5+ MSCs, CAP-1002, and others
• The Gene And Cell Therapies In Rare Disorders market is expected to surge due to the disease's increasing prevalence and awareness during the forecast period. Furthermore, launching various multiple-stage Gene And Cell Therapies In Rare Disorders pipeline products will significantly revolutionize the Gene And Cell Therapies In Rare Disorders market dynamics.
Gene And Cell Therapies In Rare Disorders Overview
Cell and gene therapies are cutting-edge medical technologies with the potential to significantly improve patient care and society at large. New developments in these innovative medicines have the potential to revolutionise medicine and the ability to treat a wide range of incurable diseases.
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Gene And Cell Therapies In Rare Disorders Epidemiology
The epidemiology section provides insights into the historical, current, and forecasted epidemiology trends in the seven major countries (7MM) from 2019 to 2032. It helps to recognize the causes of current and forecasted trends by exploring numerous studies and views of key opinion leaders. The epidemiology section also provides a detailed analysis of the diagnosed patient pool and future trends.
Gene And Cell Therapies In Rare Disorders Epidemiology Segmentation:
The Gene And Cell Therapies In Rare Disorders market report proffers epidemiological analysis for the study period 2019-2032 in the 7MM segmented into:
• Total Prevalence of Gene And Cell Therapies In Rare Disorders
• Prevalent Cases of Gene And Cell Therapies In Rare Disorders by severity
• Gender-specific Prevalence of Gene And Cell Therapies In Rare Disorders
• Diagnosed Cases of Episodic and Chronic Gene And Cell Therapies In Rare Disorders
Download the report to understand which factors are driving Gene And Cell Therapies In Rare Disorders epidemiology trends @ Gene And Cell Therapies In Rare Disorders Epidemiology Forecast
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Gene And Cell Therapies In Rare Disorders Drugs Uptake and Pipeline Development Activities
The drugs uptake section focuses on the rate of uptake of the potential drugs recently launched in the Gene And Cell Therapies In Rare Disorders market or expected to get launched during the study period. The analysis covers Gene And Cell Therapies In Rare Disorders market uptake by drugs, patient uptake by therapies, and sales of each drug.
Moreover, the therapeutics assessment section helps understand the drugs with the most rapid uptake and the reasons behind the maximal use of the drugs. Additionally, it compares the drugs based on market share.
The report also covers the Gene And Cell Therapies In Rare Disorders Pipeline Development Activities. It provides valuable insights about different therapeutic candidates in various stages and the key companies involved in developing targeted therapeutics. It also analyzes recent developments such as collaborations, acquisitions, mergers, licensing patent details, and other information for emerging therapies.
Gene And Cell Therapies In Rare Disorders Therapies and Key Companies
• Fidanacogene elaparvovec: Pfizer
• GiroctocogenE fitelparvovec: Pfizer/ Sangamo Therapeutics
• OTL-103: Orchard Therapeutics/ SR-Tiget
• OAV101: Novartis
• TVI-Brain-1: TVAX Biomedical
• AV-GBM-1: Aivita Biomedical
• ABCB5+ MSCs: RHEACELL GmbH & Co
• CAP-1002: Capricor Therapeutics
Discover more about therapies set to grab major Gene And Cell Therapies In Rare Disorders market share @ Gene And Cell Therapies In Rare Disorders Treatment Market
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Scope of the Gene And Cell Therapies In Rare Disorders Market Report
• Study Period: 2019-2032
• Coverage: 7MM [The United States, EU5 (Germany, France, Italy, Spain, and the United Kingdom), and Japan]
• Key Gene And Cell Therapies In Rare Disorders Companies: Pfizer, Sangamo Therapeutics, Orchard Therapeutics/ SR-Tiget, Novartis, TVAX Biomedical, Aivita Biomedical, RHEACELL GmbH & Co, Capricor Therapeutics, and others
• Key Gene And Cell Therapies In Rare Disorders Therapies: Fidanacogene elaparvovec, GiroctocogenE fitelparvovec, OTL-103, OAV101, TVI-Brain-1, AV-GBM-1, ABCB5+ MSCs, CAP-1002, and others
• Gene And Cell Therapies In Rare Disorders Therapeutic Assessment: Gene And Cell Therapies In Rare Disorders current marketed and Gene And Cell Therapies In Rare Disorders emerging therapies
• Gene And Cell Therapies In Rare Disorders Market Dynamics: Gene And Cell Therapies In Rare Disorders market drivers and Gene And Cell Therapies In Rare Disorders market barriers
• Competitive Intelligence Analysis: SWOT analysis, PESTLE analysis, Porter's five forces, BCG Matrix, Market entry strategies
• Gene And Cell Therapies In Rare Disorders Unmet Needs, KOL's views, Analyst's views, Gene And Cell Therapies In Rare Disorders Market Access and Reimbursement
To know more about Gene And Cell Therapies In Rare Disorders companies working in the treatment market, visit @ Gene And Cell Therapies In Rare Disorders Clinical Trials and Therapeutic Assessment
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Table of Contents
1. Gene And Cell Therapies In Rare Disorders Market Report Introduction
2. Executive Summary for Gene And Cell Therapies In Rare Disorders
3. SWOT analysis of Gene And Cell Therapies In Rare Disorders
4. Gene And Cell Therapies In Rare Disorders Patient Share (%) Overview at a Glance
5. Gene And Cell Therapies In Rare Disorders Market Overview at a Glance
6. Gene And Cell Therapies In Rare Disorders Disease Background and Overview
7. Gene And Cell Therapies In Rare Disorders Epidemiology and Patient Population
8. Country-Specific Patient Population of Gene And Cell Therapies In Rare Disorders
9. Gene And Cell Therapies In Rare Disorders Current Treatment and Medical Practices
10. Gene And Cell Therapies In Rare Disorders Unmet Needs
11. Gene And Cell Therapies In Rare Disorders Emerging Therapies
12. Gene And Cell Therapies In Rare Disorders Market Outlook
13. Country-Wise Gene And Cell Therapies In Rare Disorders Market Analysis (2019-2032)
14. Gene And Cell Therapies In Rare Disorders Market Access and Reimbursement of Therapies
15. Gene And Cell Therapies In Rare Disorders Market Drivers
16. Gene And Cell Therapies In Rare Disorders Market Barriers
17. Gene And Cell Therapies In Rare Disorders Appendix
18. Gene And Cell Therapies In Rare Disorders Report Methodology
19. DelveInsight Capabilities
20. Disclaimer
21. About DelveInsight
Related Reports:
Gene And Cell Therapies In Rare Disorders Epidemiology https://www.delveinsight.com/report-store/gene-and-cell-therapies-in-rare-disorder-epidemiology-forecast?utm_source=openpr&utm_medium=pressrelease&utm_campaign=gpr
DelveInsight's 'Gene And Cell Therapies In Rare Disorders Epidemiology Forecast to 2032' report delivers an in-depth understanding of the disease, historical and forecasted Gene And Cell Therapies In Rare Disorders epidemiology in the 7MM, i.e., the United States, EU5 (Germany, Spain, Italy, France, and the United Kingdom), and Japan.
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DelveInsight is a leading Healthcare Business Consultant, and Market Research firm focused exclusively on life sciences. It supports Pharma companies by providing comprehensive end-to-end solutions to improve their performance.
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