Tay-Sachs Disease Pipeline, Clinical Trials Assessment, NDA Approvals 2023 (Updated)

(Albany, United States) As per DelveInsight's assessment, globally, the Tay-Sachs Disease pipeline constitutes 5+ key companies continuously working towards developing 5+ Tay-Sachs Disease treatment therapies, analysis of Clinical Trials, Therapies, Mechanism of Action, Route of Administration, and Developments analysis DelveInsight.

In the Tay-Sachs Disease pipelin report, detailed description of the drug is given which includes mechanism of action of the drug, clinical studies, NDA approvals (if any), and product development activities comprising the technology, Tay-Sachs Disease collaborations, licensing, mergers and acquisition, funding, designations and other product related details.

To explore more information on the latest breakthroughs in the Tay-Sachs Disease pipeline treatment landscape of the report, click here @ Tay-Sachs Disease Pipeline Outlook- https://www.delveinsight.com/report-store/tay-sachs-disease-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Key Takeaways from the Tay-Sachs Disease Pipeline Report
• DelveInsight's Tay-Sachs Disease Pipeline analysis depicts a robust space with 5+ active players working to develop 5+ pipeline treatment therapies.
• The leading Tay-Sachs Disease Companies working in the market include Sanofi Genzyme, Sio Gene Therapies, IntraBio Inc., Taysha Gene Therapies Inc., Polaryx Therapeutics, Allievex Corporation, and others.
• Promising Tay-Sachs Disease Pipeline Therapies in the various stages of development include venglustat GZ402671, AZ-3102 (Dose 1), IB1001, miglustat, Zavesca (Miglustat), and others.
• On March 2023, IntraBio Inc. announced a study of phase 2 clinical trials for IB1001. This is a multinational, multicenter, open-label, rater-blinded prospective Phase II study which will assess the safety and efficacy of N-Acetyl-L-Leucine (IB1001) for the treatment of GM2 Gangliosidosis (Tay-Sachs and Sandhoff Disease).
• On May 2023, Dr. Anupam Sehgal announced a study of phase 1 & 2 clinical trials for TSHA-101. GM2 gangliosidoses are a group of autosomal recessive neurodegenerative diseases characterized by a deficiency of the Hex A enzyme to catabolize GM2, thereby causing GM2 accumulation within cellular lysosomes.Hex A is composed of 2 subunits, α- and β-, coded by the HEXA and HEXB genes, respectively. The primary purpose of the current study is to assess the safety and tolerability of TSHA101 administered via IT injection.
• On July 2023, Azafaros A.G. announced a study of phase 2 clinical trials for AZ-3102 (Dose 1) and AZ-3102 (Dose 2). This phase 2 is a randomized, double-blind, placebo controlled, 12 weeks study with daily oral administration of AZ-3102 aiming to evaluate the safety and pharmacokinetic (PK) profile in GM2 Gangliosidosis and Niemann-Pick type C disease (NP-C) patients. If approved by the country health authorities, a double-blind extension period will be proposed to the patients who complete the 12-week study.

Tay-Sachs Disease Overview
Tay-Sachs disease is a rare, neurodegenerative disorder in which deficiency of an enzyme (hexosaminidase A) results in excessive accumulation of certain fats (lipids) known as gangliosides in the brain and nerve cells. This abnormal accumulation of gangliosides leads to progressive dysfunction of the central nervous system. Tay-Sachs disease is categorized as a lysosomal storage disease.

To explore more information on the latest breakthroughs in the Tay-Sachs Disease Pipeline treatment landscape of the report, click here @ https://www.delveinsight.com/sample-request/tay-sachs-disease-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Tay-Sachs Disease Emerging Drugs Profile
• Venglustat: Sanofi Genzyme
• AXO-AAV-GM2: Sio Gene Therapies

Tay-Sachs Disease Pipeline Therapeutics Assessment
There are approx. 5+ key companies which are developing the therapies for Tay-Sachs Disease. The companies which have their Tay-Sachs Disease drug candidates in the most advanced stage, i.e. phase III include, Sanofi Genzyme.

Request a sample and discover the recent advances in Tay-Sachs Disease Ongoing Clinical Trial Analysis and Medications, click here @ https://www.delveinsight.com/sample-request/tay-sachs-disease-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Tay-Sachs Disease Drugs and Companies
• IB1001: IntraBio Inc.
• Miglustat: The Hospital for Sick Children
• venglustat GZ402671: Genzyme, a Sanofi
• AZ-3102 (Dose 1): Azafaros A.G

Tay-Sachs Disease Therapeutics Assessment
• Assessment by Stage and Product Type
• Assessment by Route of Administration
• Assessment by Stage and Route of Administration
• Assessment by Molecule Type
• Assessment by Stage and Molecule Type

Some of the Companies in the Tay-Sachs Disease Therapeutics Market include-
Sanofi Genzyme, Sio Gene Therapies, IntraBio Inc., Taysha Gene Therapies Inc., Polaryx Therapeutics, Allievex Corporation, and others

Dive deep into rich insights for drugs for Tay-Sachs Disease Pipeline, click here for Tay-Sachs Disease Unmet Needs and Analyst Views @ https://www.delveinsight.com/sample-request/tay-sachs-disease-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Scope of the Tay-Sachs Disease Pipeline Report
• Coverage- Global
• Tay-Sachs Disease Companies- Sanofi Genzyme, Sio Gene Therapies, IntraBio Inc., Taysha Gene Therapies Inc., Polaryx Therapeutics, Allievex Corporation, and others
• Tay-Sachs Disease Pipeline Therapies- venglustat GZ402671, AZ-3102 (Dose 1), IB1001, miglustat, Zavesca (Miglustat), and others.
• Tay-Sachs Disease Segmentation: Product Type, Molecule Type, Route of Administration

Got Queries? Find out the related information on Tay-Sachs Disease Mergers and acquisitions, Licensing Activities @ https://www.delveinsight.com/sample-request/tay-sachs-disease-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Table of Content
1. Introduction
2. Executive Summary
3. Tay-Sachs Disease: Overview
4. Pipeline Therapeutics
5. Therapeutic Assessment
6. Tay-Sachs Disease - DelveInsight's Analytical Perspective
7. Late Stage Products (Phase III)
8. Venglustat: Sanofi Genzyme
9. Drug profiles in the detailed report…..
10. Early Stage Products (Phase I/II)
11. AXO-AAV-GM2: Sio Gene Therapies
12. Drug profiles in the detailed report…..
13. Inactive Products
14. Tay-Sachs Disease Key Companies
15. Tay-Sachs Disease Key Products
16. Tay-Sachs Disease- Unmet Needs
17. Tay-Sachs Disease- Market Drivers and Barriers
18. Tay-Sachs Disease- Future Perspectives and Conclusion
19. Tay-Sachs Disease Analyst Views
20. Tay-Sachs Disease Key Companies
21. Appendix

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DelveInsight is a leading healthcare-focused market research and consulting firm that provides clients with high-quality market intelligence and analysis to support informed business decisions. With a team of experienced industry experts and a deep understanding of the life sciences and healthcare sectors, we offer customized research solutions and insights to clients across the globe. Connect with us to get high-quality, accurate, and real-time intelligence to stay ahead of the growth curve.

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