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Sickle Cell Disease Pipeline Analysis (2023) Covering Clinical Trials, Emerging Therapies, FDA, EMA, and PMDA Approvals, Competitive Landscape | Cellectis, CSL Behring, Pfizer, Aruvant, Novartis, Agios Pharma, Alfasigma, Novo Nordisk, bluebird bio

10-17-2023 07:26 PM CET | Health & Medicine

Press release from: DelveInsight Business Research LLP

Sickle Cell Disease Pipeline Analysis (2023) Covering Clinical

Las Vega (Nevada), United States //- As per DelveInsight's assessment, globally, about 40+ key pharma and biotech companies are working on 50+ pipeline drugs in the Sickle Cell Disease therapeutics landscape based on different Routes of Administration (ROA), Mechanism of Action (MOA), and molecule types. Several of the therapies are in the advanced stages of clinical development and are expected to launch in the coming years.

"Sickle Cell Disease Pipeline Insight, 2023" report by DelveInsight provides a comprehensive analysis of the ongoing clinical development activities and growth prospects across the Sickle Cell Disease Therapeutics Market.

The report provides a detailed description of the Sickle Cell Disease drugs, including the mechanism of action, type, stage, route of administration, molecule type, clinical studies, inactive pipeline products, and NDA approvals (if any). The report also covers commercial and clinical activities of the pipeline products from the pre-clinical developmental phase to the marketed stage. Additionally, it presents the ongoing developments in the therapeutics segment, including collaborations, licensing, mergers & acquisitions (M&A), funding, designations, and other product-related details.

Get a Detailed Overview of the Sickle Cell Disease Clinical Trial Activities and Regulatory Developments in the domain @
https://www.delveinsight.com/report-store/sickle-cell-disease-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=rpr

Sickle Cell Disease Pipeline Analysis
The report provides insights into:
• The report provides detailed insights into the key companies that are developing Sickle Cell Disease therapies.
• The report also evaluates different therapeutic candidates segmented into early-stage, mid-stage, and late-stage of development for Sickle Cell Disease treatment.
• It analyzes the key companies involved in targeted therapeutics development with respective active and inactive (dormant or discontinued) projects.
• It navigates the emerging Sickle Cell Disease drugs under development based on the stage of development, route of administration, target receptor, monotherapy or combination therapy, a different mechanism of action, and molecular type.
• Detailed analysis of collaborations (company-company collaborations and company-academia collaborations), licensing agreement, and financing details for future advancement in the Sickle Cell Disease treatment market.

Learn More about the Clinical and Commercial Development Activities in the Sickle Cell Disease Therapeutics Domain @
https://www.delveinsight.com/report-store/sickle-cell-disease-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=rpr

Sickle Cell Disease Therapeutics Analysis
SCD is a complex, multisystem condition characterized by acute and chronic complications. Advances in general medical care, early diagnosis, and comprehensive treatment have led to substantial improvements in the life expectancy of individuals with SCA in high-income countries, as almost all patients survive beyond 18 years of age.

In general, about half of the patients go for blood transfusions and exchanges. These are also associated with certain complications, like pain during insertions and the development of antibodies to blood types used in transfusions, and can lead to certain high levels of iron in the blood, which can cause organ damage. Thus, iron chelators are used in the latter case. Bone marrow transplants have equal positive as well as negative attributes. Currently, three therapies modify the disease course of SCA: hydroxycarbamide, erythrocyte transfusion, and hematopoietic stem cell transplantation.

There are approx. 40+ key companies developing therapies for Sickle Cell Disease (SCD). Currently, Vertex Pharmaceuticals is leading the therapeutics market with its Sickle Cell Disease (SCD) drug candidates in the most advanced stage of clinical development.

Sickle Cell Disease Companies in the Therapeutics Market Include:
Cellectis, Sana Biotechnology, Global Blood Therapeutics, Inc., CSL Behring, Pfizer, Aruvant Sciences, Graphite Bio, Novartis, Agios Pharmaceuticals, Forma Therapeutics, Vertex Pharmaceuticals, Global Blood Therapeutics, Inc., Alfasigma, Novo Nordisk, bluebird bio, ExCellThera, Gamida Cell, KM Biologics/Takeda, Editas Medicine, and many others

Emerging and Marketed Sickle Cell Disease Therapies Covered in the Report Include:
• BPX-501 T cells: Bellicum Pharmaceuticals
• Canakinumab: Novartis
• EPI01: Novo Nordisk
• CTX001: Vertex Pharmaceuticals
And Many More

Get an in-depth Assessment of the Emerging Therapies and Sickle Cell Disease Companies Actively Working in the Market @
https://www.delveinsight.com/sample-request/sickle-cell-disease-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=rpr

The Report Covers the Emerging Sickle Cell Disease Therapies Under Different Phases of Clinical Development Like -
• Late-stage products (Phase III)
• Mid-stage products (Phase II)
• Early-stage product (Phase I)
• Pre-clinical and Discovery stage candidates
• Discontinued and inactive candidates

Route of Administration
Sickle Cell Disease (SCD) pipeline report provides the therapeutic assessment of the pipeline drugs by the Route of Administration. Products have been categorized under various ROAs such as
• Intranasal
• Intrathecal
• Intravenous
• Oral
• Oral/Intravenous
• Parenteral
• Subcutaneous
• Subcutaneous/Intramuscular
• Transdermal

Molecule Type
Products have been categorized under various Molecule types such as
• Antisense oligonucleotide
• Gene therapy
• Hormones
• Neuropeptides
• Oligonucleotides
• Small Molecule
• Triglyceride

Request for Sample PDF to Understand More About the Sickle Cell Disease Treatment Outlook and Future Perspectives @
https://www.delveinsight.com/sample-request/sickle-cell-disease-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=rpr

Table of Content
1. Report Introduction
2. Executive Summary
3. Sickle Cell Disease Current Treatment Patterns
4. Sickle Cell Disease - DelveInsight's Analytical Perspective
5. Therapeutic Assessment
6. Sickle Cell Disease Late-Stage Products (Phase-III)
7. Sickle Cell Disease Mid-Stage Products (Phase-II)
8. Early Stage Products (Phase-I)
9. Pre-clinical Products and Discovery Stage Products
10. Inactive Products
11. Dormant Products
12. Sickle Cell Disease Discontinued Products
13. Sickle Cell Disease Product Profiles
14. Sickle Cell Disease Companies
15. Sickle Cell Disease Drugs
16. Dormant and Discontinued Products
17. Sickle Cell Disease Unmet Needs
18. Sickle Cell Disease Future Perspectives
19. Sickle Cell Disease Analyst Review
20. Appendix
21. Report Methodology

Get Detailed Insights About the Reports Offerings @
https://www.delveinsight.com/sample-request/sickle-cell-disease-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=rpr

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Email: info@delveinsight.com

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About DelveInsight
DelveInsight is a leading Business Consultant and Market Research firm focused exclusively on life sciences. It supports Pharma companies by providing comprehensive end-to-end solutions to improve their performance.

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