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Friedreich's Ataxia Pipeline, Clinical Trials Assessment, NDA Approvals 2023 (Updated) | PTC Therapeutics, Retrotope, Reata Pharmaceuticals, Minoryx Therapeutics, Larimar Therapeutics, and others

07-21-2023 07:30 AM CET | Health & Medicine

Press release from: DelveInsight Business Research

(Albany, United States) As per DelveInsight's assessment, globally, the Friedreich's Ataxia pipeline constitutes 10+ key companies continuously working towards developing 10+ Friedreich's Ataxia treatment therapies, analysis of Clinical Trials, Therapies, Mechanism of Action, Route of Administration, and Developments analysis DelveInsight.

In the Friedreich's Ataxia Pipeline Report, detailed description of the drug is given which includes mechanism of action of the drug, clinical studies, Friedreich's Ataxia NDA approvals (if any), and product development activities comprising the technology, Friedreich's Ataxia collaborations, licensing, mergers and acquisition, funding, designations and other product related details.

To explore more information on the latest breakthroughs in the Friedreich's Ataxia pipeline treatment landscape of the report, click here @ Friedreich's Ataxia Pipeline- https://www.delveinsight.com/report-store/friedreich-ataxia-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Key Takeaways from the Friedreich's Ataxia Pipeline Report
• DelveInsight's Friedreich's Ataxia Pipeline analysis depicts a robust space with 10+ active players working to develop 10+ pipeline treatment therapies.
• The leading Friedreich's Ataxia Companies working in the market include PTC Therapeutics, Retrotope, Reata Pharmaceuticals, Minoryx Therapeutics, Larimar Therapeutics, LEXEO Therapeutics, Exicure, StrideBio, Voyager Therapeutics, Lacerta Therapeutics, and others
• Promising Friedreich's Ataxia Pipeline Therapies in the various stages of development include TAK-831, Omaveloxolone Capsules, 2.5 mg, MIN-102, Deferiprone oral solution 100mg/mL, MIB-626, Vatiquinone, DT-216, deferiprone, RT001, Idebenone, and others.
• On July 2023, Metro International Biotech LLC announced a study of phase 2 clinical trials for MIB-626. The primary objective is to test the safety and tolerability of short-term therapy with a nicotinamide adenine dinucleotide (NAD+) precursor (MIB-626) in adults with Friedreich's Ataxia (FA) without overt heart failure and with a left ventricular ejection fraction ≥ 40%. A key secondary objective is to test the effects of MIB-626 on cardiac and skeletal muscle bioenergetics.
• On July 2023, PTC Therapeutics announced a study of phase 3 clinical trials for Vatiquinone. The primary objective of this study is to assess the long-term safety of vatiquinone in participants with Friedreich ataxia (FA) previously exposed to vatiquinone in Study PTC743-NEU-003-FA (NCT04577352) or Study PTC743-NEU-005-FA.
• On March 2023, Design Therapeutics Inc announced a study of phase 1 clinical trials for DT-216. The purpose of this study is to evaluate the safety, tolerability, pharmacokinetic and pharmacodynamic effects of intravenous DT-216 in adult patients with Friedreich Ataxia. This single ascending dose study is randomized, double-blind, placebo-controlled.

Friedreich's Ataxia Overview
Friedreich's Ataxia (FRDA) is a genetic, progressive, neurodegenerative movement disorder, with a typical age of onset between 10 and 15 years. Initial symptoms may include unsteady posture, frequent falling, and progressive difficulty in walking due to impaired ability to coordinate voluntary movements (ataxia).

To explore more information on the latest breakthroughs in the Friedreich's Ataxia Pipeline treatment landscape of the report, click here @ https://www.delveinsight.com/sample-request/friedreich-ataxia-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Friedreich's Ataxia Emerging Drugs Profile
• RT 001: Retrotope
• Leriglitazone: Minoryx Therapeutics

Friedreich's Ataxia Pipeline Therapeutics Assessment
There are approx. 10+ key companies which are developing the Friedreich's Ataxia. The Friedreich's Ataxia companies which have their Friedreich's Ataxia drug candidates in the most advanced stage, i.e. Phase III include, Retrotope.

Request a sample and discover the recent advances in Friedreich's Ataxia Ongoing Clinical Trial Analysis and Medications, click here @ https://www.delveinsight.com/sample-request/friedreich-ataxia-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Friedreich's Ataxia Drugs and Companies
• TAK-831: Neurocrine Biosciences
• Omaveloxolone Capsules, 2.5 mg: Reata Pharmaceuticals Inc
• MIN-102: Minoryx Therapeutics S.L.
• Deferiprone oral solution 100mg/mL: ApoPharma
• MIB-626: Metro International Biotech LLC
• Vatiquinone: PTC Therapeutics

Friedreich's Ataxia Therapeutics Assessment
• Assessment by Stage and Product Type
• Assessment by Route of Administration
• Assessment by Stage and Route of Administration
• Assessment by Molecule Type
• Assessment by Stage and Molecule Type

Some of the Companies in the Friedreich's Ataxia Therapeutics Market include-
PTC Therapeutics, Retrotope, Reata Pharmaceuticals, Minoryx Therapeutics, Larimar Therapeutics, LEXEO Therapeutics, Exicure, StrideBio, Voyager Therapeutics, Lacerta Therapeutics, and others.

Dive deep into rich insights for drugs for Friedreich's Ataxia Pipeline, click here for Friedreich's Ataxia Unmet Needs and Analyst Views @ https://www.delveinsight.com/sample-request/friedreich-ataxia-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Scope of the Friedreich's Ataxia Pipeline Report
• Coverage- Global
• Friedreich's Ataxia Companies- PTC Therapeutics, Retrotope, Reata Pharmaceuticals, Minoryx Therapeutics, Larimar Therapeutics, LEXEO Therapeutics, Exicure, StrideBio, Voyager Therapeutics, Lacerta Therapeutics, and others.
• Friedreich's Ataxia Pipeline Therapies- TAK-831, Omaveloxolone Capsules, 2.5 mg, MIN-102, Deferiprone oral solution 100mg/mL, MIB-626, Vatiquinone, DT-216, deferiprone, RT001, Idebenone, and others.
• Friedreich's Ataxia Pipeline Segmentation: Product Type, Molecule Type, Route of Administration

Got Queries? Find out the related information on Friedreich's Ataxia Mergers and acquisitions, Licensing Activities @ https://www.delveinsight.com/sample-request/friedreich-ataxia-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Table of Content
1. Introduction
2. Executive Summary
3. Friedreich's Ataxia: Overview
4. Pipeline Therapeutics
5. Therapeutic Assessment
6. Friedreich's Ataxia- DelveInsight's Analytical Perspective
7. In-depth Commercial Assessment
8. Friedreich's Ataxia Collaboration Deals
9. Late Stage Products (Phase III)
10. RT 001: Retrotope
11. Drug profiles in the detailed report…..
12. Mid Stage Products (Phase II)
13. Leriglitazone: Minoryx Therapeutics
14. Drug profiles in the detailed report…..
15. Early Stage Products (Phase I)
16. CTI-1601: Larimar Therapeutics
17. Drug profiles in the detailed report…..
18. Preclinical and Discovery Stage Products
19. LX-2006: LEXEO Therapeutics
20. Drug profiles in the detailed report…..
21. Inactive Products
22. Friedreich's Ataxia Key Companies
23. Friedreich's Ataxia Key Products
24. Friedreich's Ataxia- Unmet Needs
25. Friedreich's Ataxia- Market Drivers and Barriers
26. Friedreich's Ataxia- Future Perspectives and Conclusion
27. Friedreich's Ataxia Analyst Views
28. Friedreich's Ataxia Key Companies
29. Appendix

About Us

DelveInsight is a Business Consulting and Market research company, providing expert business solutions for the healthcare domain and offering quintessential advisory services in the areas of R&D, Strategy Formulation, Operations, Competitive Intelligence, Competitive Landscaping, and Mergers & Acquisitions.

Company Name: DelveInsight Business Research LLP
Contact Person: Yash Bhardwaj
Email: ybhardwaj@delveinsight.com
Phone: 9193216187
Address: 304 S. Jones Blvd #2432
City: Las Vegas
State: NV
Country: United States
Website: https://www.delveinsight.com/

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