Galactosemia Market to Expand at a Significant Growth Rate During the Forecast Period (2023-32) - Estimates DelveInsight | Jaguar Gene Therapy (JAG 101), Applied therapeutics (AT-007), BridgeBio Pharma

DelveInsight's "Galactosemia Market Insights, Epidemiology, and Market Forecast 2032" report delivers an in-depth understanding of the disease, historical and forecasted epidemiology, as well as the Galactosemia Market Size and Share in the seven major markets (7MM) (i.e., the United States, EU4 (Germany, Spain, Italy, France), the United Kingdom and Japan).

The market report covers emerging drugs, treatment practices, market share of individual Galactosemia therapies, and current & forecasted market size from 2019 to 2032. It also evaluates the current Galactosemia treatment practice/algorithm, market drivers & barriers, and unmet medical needs to curate the best of opportunities and assess the underlying potential of the market.

Galactosemia: An Overview
Galactosemia is a rare genetic disorder characterized by the body's inability to properly metabolize galactose, a sugar found in milk and other dairy products. This is caused by a deficiency or absence of certain enzymes needed to break down galactose into glucose, leading to an accumulation of galactose in the body, which can be toxic.

Galactosemia is considered a rare disorder, and its prevalence varies depending on the population. In general, it is estimated to occur in approximately 1 in 30,000 to 60,000 births worldwide. However, the prevalence may be higher in certain ethnic groups due to genetic variations.

Early diagnosis and treatment with a lactose-restricted (dairy-free) diet are absolutely essential to avoid profound intellectual disability, liver failure, and death in the newborn period. Galactosemia is typically diagnosed shortly after birth through newborn screening programs, where a small blood sample is taken from a baby's heel to test for various genetic conditions. If galactosemia is suspected, further testing is done to confirm the diagnosis. It is essential to diagnose and start treatment as early as possible to prevent severe complications.

The primary treatment for galactosemia involves a strict galactose-free diet. Since galactose is commonly found in dairy products, affected individuals must avoid milk, cheese, butter, and other galactose-containing foods. Instead, they can use lactose-free formulas and carefully selected foods. Nutritional support is crucial to ensure the person receives adequate nutrients for growth and development. If galactosemia is detected early and managed effectively with a proper diet, individuals with the condition can lead relatively healthy lives without significant complications. However, even with appropriate dietary restrictions, some individuals may experience long-term issues, such as speech and language delays, learning difficulties, and fertility problems.

In some severe cases, where the restriction of galactose in the diet is not sufficient, additional medications or treatments may be required. As with any medical condition, it is essential for affected individuals to work closely with healthcare professionals experienced in managing galactosemia to optimize their treatment and care.

Discover How Galactosemia Market Will Grow by 2032:
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Galactosemia Market
The market outlook section of the report helps to build a detailed comprehension of the historical, current, and forecasted market size by analyzing the impact of current and emerging Galactosemia therapies in the market. It also provides a detailed assessment of the Galactosemia market drivers & barriers, unmet needs, and emerging technologies.

The report gives complete detail of the market trend for each marketed Galactosemia drug and late-stage pipeline therapies by evaluating their impact based on the annual cost of therapy, inclusion and exclusion criteria, mechanism of action (MOA), competition with other therapies, brand value, their impact on the market and view of the key opinion leaders.

Galactosemia Epidemiology
The epidemiology section covers detailed insights into the historical, and current Galactosemia patient pool and forecasted epidemiology trends for every seven major countries (7MM) from 2019 to 2032.

Get Key Insights Into the Evolving Galactosemia Epidemiology Trends @
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Galactosemia Drugs Uptake and Pipeline Development Activities
The drugs' uptake section focuses on the rate of uptake of the potential drugs recently launched in the Galactosemia market or expected to be launched during the study period. The analysis covers the market share by Galactosemia drugs, patient uptake by therapies, and sales of each drug.

The report's drugs uptake section helps in understanding the drugs with the most rapid uptake and the reasons behind the maximal use of new drugs. It allows the comparison of the drugs based on market share and size, which again will be helpful in investigating factors important in understanding the market dynamics and in making financial and regulatory decisions.

The report also covers the Galactosemia Pipeline Development Activities and provides valuable insights about different therapeutic candidates in Phase II and Phase III stages and the key companies in the market involved in developing targeted therapeutics. It also analyses recent developments such as collaborations, acquisitions, mergers, licensing patent details, and other information for emerging therapies.

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Galactosemia Therapeutics Assessment
Several major pharma and biotech companies are developing therapies for Galactosemia. Currently, Applied Therapeutics is leading the therapeutics market with its Galactosemia drug candidates in the most advanced stage of clinical development.

Leading Companies in the Galactosemia Therapeutics Market Include
• Applied therapeutics
• Jaguar Gene Therapy
• BridgeBio Pharma
And Many Others

Emerging and Marketed Galactosemia Therapies Covered in the Report Include
• AT-007: Applied therapeutics
AT-007 is an investigational, novel Aldose Reductase Inhibitor (ARI) being developed for the treatment of several rare diseases. AT-007 is a potent and selective compound, which crosses the blood brain barrier into the Central Nervous System (CNS penetrant). AT-007 has received both Orphan Drug and Pediatric Rare Disease designations from the FDA for the treatment of Galactosemia, a rare metabolic disease, and Phosphomannomutase 2 Deficiency - a Congenital Disorder of Glycosylation (PMM2-CDG).

• JAG 101: Jaguar Gene Therapy
Jaguar is advancing JAG101, an investigational gene therapy currently in preclinical development that aims to deliver a gene replacement solution to address the root cause of Type 1 galactosemia by delivering the functional GALT gene via the AAV9 vector.

Learn More About the Emerging Therapies & Key Companies in the Galactosemia Therapeutics Market:
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Table of Content (TOC)
1. Key Insights
2. Executive Summary
3. Galactosemia Competitive Intelligence Analysis
4. Galactosemia Market Overview at a Glance
5. Galactosemia Background and Overview
6. Galactosemia Patient Journey
7. Galactosemia Epidemiology and Patient Population
8. Galactosemia Treatment Algorithm, Current Treatment, and Medical Practices
9. Galactosemia Unmet Needs
10. Key Endpoints of Galactosemia Treatment
11. Galactosemia Marketed Products
12. Galactosemia Emerging Therapies
13. Galactosemia Seven Major Market Analysis
14. Attribute Analysis
15. Galactosemia Market Outlook (7 major markets)
16. Galactosemia Access and Reimbursement Overview
17. KOL Views on the Galactosemia Market.
18. Galactosemia Market Drivers
19. Galactosemia Market Barriers
20. Appendix
21. DelveInsight Capabilities
22. Disclaimer
*The table of contents is not exhaustive; the final content may vary.

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