Comprehensive Analysis On United Kingdom Mucopolysaccharidosis VI (MPS VI) Therapeutics Market 2023 With Future Trend, Market Size, Business Growth, Top Key players, CAGR

Report Overview

The UK Mucopolysaccharidosis VI Therapeutics market size stood at around USD xx billion in 2020 and is projected to reach USD xx billion by 2028, exhibiting a CAGR of xx% during the forecast period.

Mucopolysaccharidosis VI (MPS VI), also known as Maroteaux-Lamy syndrome is a member of a group of hereditary metabolic diseases known as the mucopolysaccharidoses which, in turn, are part of a larger group of diseases known as lysosomal storage disorders (LSDs). MPS VI is a rare genetic disorder characterized by a complete or partial lack of activity of the enzyme arylsulfatase B (also called N-acetylgalactosamine-4-sulfatase), encoded by the ARSB gene. MPS VI occurs due to mutations in theARSBgene and is inherited as an autosomal recessive disorder. The deficiency or absence of this enzyme activity leads to the accumulation of complex carbohydrates called glycosaminoglycans (previously known as mucopolysaccharides) in the body. Abnormal accumulation of mucopolysaccharides leads to progressive involvement of multiple organ systems.

The symptoms and severity of Maroteaux-Lamy syndrome can vary dramatically from one person to another; some individuals only develop mild symptoms, while others develop severe, even life-threatening complications. Common symptoms can include coarse facial features, corneal clouding, joint abnormalities, various skeletal malformations, an abnormally enlarged liver and/or spleen (hepatosplenomegaly), and hearing loss. It is estimated that nearly 6% of the UK population (around 3.5 million people) will be affected by a rare disease at some point in their lives, and the MPS VI had the highest birth prevalence of 7.85 per 100,000 live births, comprising 46% of all MPS cases diagnosed.

Initial diagnosis is usually made between 6 and 24 months of age, and life expectancy depends on the severity of symptoms and is around 20 to 30 years. People with MPS VI often begin to show signs and symptoms of MPS VI during early childhood, these include changes to the physical appearance as well as developing other clinical features in the cardiovascular and respiratory systems. Importantly, MPS VI does not affect intelligence.

Market Growth Drivers

The growth in the number of products in the preliminary and advanced stages of R&D along with the focus on the treatment of Maroteaux-Lamy syndrome is anticipated to drive the growth in the MPS VI treatment market at a considerably fast rate. With the approval of BioMarins Naglazyme (galsulfase), the market is expected to be boosted several products currently in the pipeline of various companies can be anticipated to undergo regulatory approvals for the marketing, if they have favorable clinical trials results.

The increasing incidence and prevalence also boost the MPS VI treatment market growth during the forecast period. Market players are more focused on the adoption of inorganic growth strategies such as collaborations and partnerships to strengthen their position in the MPS VI treatment market. The adoption of inorganic growth strategies by key players is expected to drive the market growth over the forecast period.

Market Restraints

However, rising treatment costs and a lack of awareness among patients and physicians about MPS VI are among the major factors acting as restraints and will continue to pose a challenge to the MPS VI treatment market in the forecast period.

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Top Major Players

The UK MPS VI therapeutics market is highly competitive, as many of the players are well engaged to deliver the best therapeutic solution for the treatment of Maroteaux-Lamy syndrome. The prominent players in the market have adopted various strategies to garner maximum market share. BioMarin's Naglazyme (galsulfase) has been approved as the enzyme replacement therapy for the treatment of Maroteaux-Lamy syndrome. Thus, the key players are anticipated to have lucrative growth opportunities in the future with the rising demand for MPS VI treatment. Major players operating in the MPS VI treatment market include BioMarin Pharmaceuticals Inc, Inventiva Pharma, Fondazione Telethon, and Genzyme Corporation among others.

The United Kingdom Mucopolysaccharidosis VI (MPS VI) Therapeutics Market 2023 Report makes available the current and forthcoming technical and financial details of the industry. It is one of the most comprehensive and important additions to the Prudent Markets archive of market research studies. It offers detailed research and analysis of key aspects of the global United Kingdom Mucopolysaccharidosis VI (MPS VI) Therapeutics market. This report explores all the key factors affecting the growth of the global United Kingdom Mucopolysaccharidosis VI (MPS VI) Therapeutics market, including demand-supply scenario, pricing structure, profit margins, production, and value chain analysis.

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Market Segmentation

By Therapeutics:

On the basis of therapeutics, the MPS VI therapeutics market can be segmented into
Enzyme Replacement Therapies (ERT)
Hematopoietic Stem Cell Transplantation (HSCT)
Gene Therapy
Others

ERT consists of replacing the deficient or absent enzyme with a functional recombinant version through intravenous administration. At present, enzyme replacement therapy accounts for the largest proportion of the market, and the trend is expected to remain the same during the forecast period.

By Route of Administration:

Based on the route of administration, the MPS VI therapeutics market can be segmented into

Oral
Intravenous (IV)
Others

The intravenous type is anticipated to account for the majority of the revenue share of the route of administration segment. Because Naglazyme (galsulfase) is the most preferred therapeutic which is given as an intravenous infusion. Therefore, further projected to control its market share during the forecast period.

By Distribution Channels:

In terms of distribution channels, the MPS VI therapeutics market can be bifurcated into

Hospital pharmacies
Retail pharmacies
Online pharmacies

The hospitals have amassed the most share of the market due to their widespread presence and the preference for hospitals among patients. Thus, the hospital segment is anticipated for robust growth during the forecast period.

By End Users:

Based on end-user, the MPS VI therapeutics market can be segmented into

Hospitals
Specialty Clinics
Medical Research Centres
Home-infusion
Others

Naglazyme (galsulfase) is the best solution for Maroteaux-Lamy syndrome which is given as a weekly infusion lasting about 4 hours that can be administered at home. Thus, the potential growth of home infusion can be anticipated during the forecast period.

Top Major Players

The UK MPS VI therapeutics market is highly competitive, as many of the players are well engaged to deliver the best therapeutic solution for the treatment of Maroteaux-Lamy syndrome. The prominent players in the market have adopted various strategies to garner maximum market share. BioMarin's Naglazyme (galsulfase) has been approved as the enzyme replacement therapy for the treatment of Maroteaux-Lamy syndrome. Thus, the key players are anticipated to have lucrative growth opportunities in the future with the rising demand for MPS VI treatment. Major players operating in the MPS VI treatment market include BioMarin Pharmaceuticals Inc, Inventiva Pharma, Fondazione Telethon, and Genzyme Corporation among others.

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The report covers the competitive analysis of the market. As the demand is driven by a buyer's paying capacity and the rate of item development, the report shows the important regions that will direct growth. This section exclusively shares insight into the budget reports of big-league members of the market helping key players and new entrants understand the potential of investments in the Global United Kingdom Mucopolysaccharidosis VI (MPS VI) Therapeutics Market. It can be better employed by both traditional and new players in the industry for complete know-how of the market.

Strategic Points Covered in Table of Content of Global United Kingdom Mucopolysaccharidosis VI (MPS VI) Therapeutics Market:

Chapter 1: Introduction, market driving force product Objective of Study and Research Scope the United Kingdom Mucopolysaccharidosis VI (MPS VI) Therapeutics market
Chapter 2: Exclusive Summary - the basic information of the United Kingdom Mucopolysaccharidosis VI (MPS VI) Therapeutics Market.
Chapter 3: Displaying the Market Dynamics- Drivers, Trends and Challenges & Opportunities of the United Kingdom Mucopolysaccharidosis VI (MPS VI) Therapeutics
Chapter 4: Presenting the United Kingdom Mucopolysaccharidosis VI (MPS VI) Therapeutics Market Factor Analysis, Porters Five Forces, Supply/Value Chain, PESTEL analysis, Market Entropy, Patent/Trademark Analysis.
Chapter 5: Displaying the by Type, End User and Region/Country
Chapter 6: Evaluating the leading manufacturers of the United Kingdom Mucopolysaccharidosis VI (MPS VI) Therapeutics market which consists of its Competitive Landscape, Peer Group Analysis, BCG Matrix & Company Profile
Chapter 7: To evaluate the market by segments, by countries and by Manufacturers/Company with revenue share and sales by key countries in these various regions
Chapter 8 & 9: Displaying the Appendix, Methodology and Data Source

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