Sandhoff Disease Treatment Market 2020 Global Updates || Leading  Players - Intrabio, Axovant Gene Therapies Ltd

Global Sandhoff disease treatment market is growing at a steady CAGR in the forecast period of 2019-2026. The report contains data of the base year 2018 and historic year 2017. This rise in market value can be attributed to the orphan drug designation to novel drugs, along with the increasing investment of biotechnology and pharmaceutical industries in R&D. The key market players in the Sandhoff disease treatment market are Intrabio, Axovant Gene Therapies Ltd among others

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The rapidly revolutionizing market place demands the best market and business solutions to thrive in the market. This Sandhoff Disease Treatment market document contains a comprehensive data of market definition, classifications, applications, engagements, market drivers and market restraints of Healthcare Industry all of which is derived from SWOT analysis. Market definition covered in this Sandhoff Disease Treatment market document gives the scope of particular product with respect to the driving factors and restraints in the market. The sources of data and information mentioned in the Sandhoff Disease Treatment market document are very reliable and include websites, annual reports of the companies, journals, and mergers which are checked and validated by the market experts.

Market Definition: Global Sandhoff Disease Treatment Market:-

Sandhoff disease is also known as Beta-hexosaminidase-beta-subunit deficiency is a fatal pediatric lysosomal storage genetic disorder characterized by progressively destruction of neuron in the brain and spinal cord. It is caused by defects in HEXB gene which is responsible for regulation of vital enzyme called beta-hexosaminidase, as a result of accumulation of lipid called G2 gangliosides. This ongoing accumulation of lipid affects the function of the nerve cells and causes other neurological problem.

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Segmentation: Global Sandhoff Disease Treatment Market:-

Sandhoff Disease Treatment Market : By Types

Infantile
Juvenile
Late Onset

Sandhoff Disease Treatment Market : By Therapy

Gene Therapy
Enzyme Replacement Therapy
Stem Cell Therapy
Others

Sandhoff Disease Treatment Market : By Treatment

Medication
Surgery

Sandhoff Disease Treatment Market : By Drugs

Anticonvulsants
Miglustat
Others

Sandhoff Disease Treatment Market : By Route of Administration

Oral
Inhalation
Parenteral

Sandhoff Disease Treatment Market : By Distribution Channel

Hospital Pharmacy
Retail Pharmacy
Online Pharmacy

Sandhoff Disease Treatment Market : By End-Users

Hospitals
Homecare
Specialty Clinics

Sandhoff Disease Treatment Market : By Geography

North America
Europe
Asia-Pacific
South America
Middle East & Africa

Key Developments in the Sandhoff Disease Treatment Market:-

In March 2019, Axovant Gene Therapies Ltd, reported clinical trial data for AXO-AAV-GM2, a gene therapy for the treatment of Tay-Sachs disease. The trial demonstrated well-tolerated with no serious adverse events, evaluated in the 30-month-old patient with advanced infantile Tay-Sachs disease. This clinical trial results leverages the expertise in the treatment of GM2 Gangliosidosis (including Tay-Sachs disease and Sandhoff disease)

In December 2018, IntraBio received the U.S FDA Rare Pediatric Disease designation for the IB1001, a novel drug for the treatment of GM2 Gangliosidosis (Tay-Sachs and Sandhoff Disease). This designation enables the company to obtain the Priority Review Voucher (PRV) which will be entitled to receive priority review providing enhanced support and optimizing the development of eligible medicines

Sandhoff Disease Treatment Market Drivers:-

Increasing awareness amongst people about genetic disorders will act as a market driver

Rise in special drug designation from the regulatory authorities  is another factor boosting the market growth

Increasing investment of biotechnology and pharmaceutical industries in R&D also acts as a market driver in the forecast period

Increase in competitive scenario among the pharmaceutical companies is expected to drive the market growth

Sandhoff Disease Treatment Market Restraints:-

Limited operating revenue opportunities for research and development of targeted therapies by many pharmaceuticals can impede the market growth

Lack of availability of essential services in remote areas is hindering the market growth

Lack of proper training and knowledge in healthcare professional will also restrict the market growth in the forecast period

Sandhoff Disease Treatment Market : Competitive Analysis:-

Global Sandhoff disease treatment market is highly fragmented and the major players have used various strategies such as new product launches, expansions, agreements, joint ventures, partnerships, acquisitions, and others to increase their footprints in this market. The report includes market shares of Sandhoff disease treatment for Global, Europe, North America, Asia-Pacific, South America and Middle East & Africa.

Opportunities in the Sandhoff Disease Treatment Market :-

To strategically profile key players and comprehensively analyze their market position in terms of ranking and core competencies, and detail the competitive landscape for market leaders

To describe and forecast of Sandhoff Disease Treatment market, in terms of value, for various segments, by region North America, Europe, Asia Pacific (APAC), and Rest of the World (RoW)

Comprehensive quantitative analysis of the industry is provided for the period of 2020-2026 to assist stakeholders to capitalize on the prevailing market opportunities.

Extensive analysis of the key segments of the industry helps in understanding the trends in types of point of care test across Europe.

To get a comprehensive overview of the Sandhoff Disease Treatment market.

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