Press release
Rare Diseases Market to Reach USD 414.62 Billion by 2034 Driven by Gene Therapies
Rare Diseases Market
Download Full PDF Sample Copy of Market Report
https://exactitudeconsultancy.com/request-sample/73179
Market Summary
The Rare Diseases Market continues to grow significantly as pharmaceutical and biotech companies intensify R&D efforts across over 7,000+ identified rare diseases, many of which still lack approved treatments. Major innovation is focused on gene therapies, AAV & lentiviral vectors, antisense oligonucleotides (ASOs), enzyme replacement therapies (ERTs), monoclonal antibodies, small molecules, and RNA-based therapeutics.
Advances in genomic sequencing and newborn screening are improving early detection, while global regulatory incentives-such as the FDA Orphan Drug Act, EMA PRIME, and Japan's Sakigake pathway-are accelerating drug development timelines. North America dominates the market, while Asia-Pacific is the fastest-growing region driven by expanding rare disease awareness and increasing access to advanced therapies.
Key Takeaways
• 2024 Market Size: USD 218.34 Billion
• 2034 Forecast: USD 414.62 Billion
• CAGR: 6.7% (2025-2034)
• Strong pipeline of gene & cell therapies targeting ultra-rare genetic disorders
• Regulatory incentives boosting orphan drug approvals globally
• Rising patient advocacy and rare disease registries improving clinical trial participation
Explore Full Report here:
https://exactitudeconsultancy.com/reports/73179/rare-diseases-market
Market Drivers
• Increasing investment in precision and genomic medicine
• Advancements in CRISPR, AAV gene therapy, and mRNA technologies
• High unmet clinical need across metabolic, neurological & genetic disorders
• Growing collaborations between biotech startups, academia, and big pharma
• Expansion of reimbursement frameworks supporting high-cost orphan drugs
Segmentation Snapshot
By Therapeutic Type
• Gene Therapy
• Enzyme Replacement Therapy (ERT)
• RNA-Based Therapies (ASOs, siRNA)
• Small Molecules
• Monoclonal Antibodies
• Others
By Disease Area
• Neurological Disorders
• Metabolic Disorders
• Hematologic Disorders
• Immunological Disorders
• Cardiovascular Rare Diseases
• Others
By End User
• Hospitals
• Specialty Clinics
• Research Institutions
• Home Healthcare (For Chronic Rare Disorders)
By Region
• North America (Largest Market)
• Europe
• Asia-Pacific (Fastest Growing)
• Latin America
• Middle East & Africa
Get Your Exclusive Offer with up to 10% Discount
https://exactitudeconsultancy.com/checkout/?currency=USD&type=single_user_license&report_id=73179
Recent Developments
• Breakthrough gene therapies approved for spinal muscular atrophy and inherited retinal disorders.
• Expansion of rare disease clinical trials driven by AI-based patient matching.
• Novel ASO therapies progressing for neurological rare disorders.
Expert Quote - Irfan Tamboli, Business Development Executive
"The rare diseases market is entering a new era powered by gene therapies and precision medicine. With increasing global awareness and strong regulatory support, innovation is finally reaching underserved patient populations."
Conclusion
The Rare Diseases Market is set for sustained growth as next-generation therapies-especially gene, RNA-based, and targeted biologics-emerge as transformative treatment options. Companies with strong orphan drug pipelines and partnerships in genomic medicine will shape the future of this high-impact healthcare segment.
This report is also available in the following languages : Japanese (希少疾患市場), Korean (희귀 질환 시장), Chinese (罕见病市场), French (Marché des maladies rares), German (Markt für seltene Krankheiten), and Italian (Mercato delle malattie rare), etc.
Request for a sample of this research report at (Use Corporate Mail ID for Quick Response) @
https://exactitudeconsultancy.com/request-sample/73179
Our More Reports:
Cytotoxic Drugs and HPAPI Manufacturing Market
https://exactitudeconsultancy.com/reports/72927/cytotoxic-drugs-and-hpapi-manufacturing-market
Ophthalmic Drugs Contract Manufacturing Market
https://exactitudeconsultancy.com/reports/72929/ophthalmic-drugs-contract-manufacturing-market
DNA Encoded Library Market
https://exactitudeconsultancy.com/reports/73115/dna-encoded-library-market
Bispecific Antibodies Market
https://exactitudeconsultancy.com/reports/73117/bispecific-antibodies-market
https://bulletin.exactitudeconsultancy.com/
https://www.thehealthanalytics.com/
https://www.analytica.global/
https://www.marketintelligencedata.com/
https://www.marketinsightsreports.com/
Connect Us:
Irfan Tamboli
PHONE NUMBER +1 (704) 266-3234
EMAIL ADDRESS: sales@exactitudeconsultancy.com
About Us
Exactitude Consultancy is a market research & consulting services firm which helps its client to address their most pressing strategic and business challenges. Our market research helps clients to address critical business challenges and also helps make optimized business decisions with our fact-based research insights, market intelligence, and accurate data.
This release was published on openPR.
Permanent link to this press release:
Copy
Please set a link in the press area of your homepage to this press release on openPR. openPR disclaims liability for any content contained in this release.
You can edit or delete your press release Rare Diseases Market to Reach USD 414.62 Billion by 2034 Driven by Gene Therapies here
News-ID: 4302417 • Views: …
More Releases from Exactitude Consultancy
Cold Planer Market Sees Consistent Growth Supported by Global Road Rehabilitatio …
The global cold planer market is experiencing steady growth as governments and private contractors increase spending on road rehabilitation, resurfacing, and infrastructure modernization. Cold planers, also known as milling machines, are widely used to remove damaged asphalt and concrete surfaces efficiently, supporting sustainable road construction practices.
Download Full PDF Sample Copy of Market Report @ https://exactitudeconsultancy.com/request-sample/68250
Key Market Highlights
• Increasing focus on road maintenance and resurfacing projects
• Growing demand for efficient and precision milling…
Credit Management Software Market Accelerates as Organizations Focus on Risk Mit …
The global credit management software market is witnessing robust growth as organizations across industries adopt digital solutions to manage credit risk, improve receivables performance, and strengthen financial controls. Credit management software enables businesses to automate credit scoring, monitor customer creditworthiness, and streamline collections processes.
Download Full PDF Sample Copy of Market Report @ https://exactitudeconsultancy.com/request-sample/68248
Key Market Highlights
• Growing adoption of automated credit risk assessment tools
• Increasing focus on working capital and cash flow management
• Integration…
Session Border Controller Market Expands Rapidly as Enterprises and Telecom Oper …
The global session border controller (SBC) market is experiencing strong growth as telecom operators and enterprises increasingly deploy SBC solutions to secure, manage, and optimize real-time IP communications. SBCs play a critical role in protecting voice over IP (VoIP), unified communications (UC), and multimedia sessions from cyber threats while ensuring interoperability and quality of service.
Download Full PDF Sample Copy of Market Report @ https://exactitudeconsultancy.com/request-sample/68246
Key Market Highlights
• Growing adoption of VoIP and…
Biofuel Market Including E-Methane and Sustainable Aviation Fuel Gains Strong Tr …
The global biofuel market, encompassing e-methane, sustainable aviation fuel (SAF), and other advanced biofuels, is witnessing robust growth as governments and industries intensify efforts to reduce carbon emissions and transition toward cleaner energy sources. These fuels play a critical role in achieving net-zero targets while enabling decarbonization of hard-to-abate sectors such as aviation, shipping, and heavy transportation.
Download Full PDF Sample Copy of Market Report @ https://exactitudeconsultancy.com/request-sample/68244
Key Market Highlights
• Rapid growth of…
More Releases for Rare
lacit Market With Industrial Analysis by Forecast 2020-2025 | China Minmetals Ra …
This report provides in-depth study on the current state of the Global Lacit Market 2020-2025. Key players in the Global Lacit Market have been identified through the secondary research and their market share has been determined through primary and secondary research.
Global Lacit Market overview:
It is a compound made from lanthanum acetate and citric acid. LaCit market is segmented by Type, and by Application. Players, stakeholders, and other participants in the…
Rare Earth Metals Market Insights, Forecast to 2024| Great Western Minerals, Ind …
Growing demand for magnets in automobiles, and energy generation will majorly contribute to the growth of global rare earth metals market over the forecast period. The demand for rare earth magnets is majorly increasing by their consumption in electric and hybrid vehicles, and wind turbines. Increasing focus on utilizing clean and renewable energy is giving a substantial pressure on the electricity providers, to generate energy through renewable sources, which in…
Global Erbium Oxide Market 2017 - Chenguang Rare Earth, Longyi Heavy Rare-Earth, …
The report studies Erbium Oxide in Global market Professional Survey 2017 : Size, Share, Trends, Industry Growth, Opportunity, Application, Production, Segmentation, Cost Structure, Company Profile, Product Picture and Specifications during the Forecast period by 2022
The report Global Erbium Oxide Industry provides a comprehensive analysis of the Erbium Oxide market. The report features industry insights from experts. A detailed segmentation of the Global Erbium Oxide market has been included in the…
Global Dysprosium Oxide Market 2017 - Longyi Heavy Rare-Earth, China Minmetals R …
The report studies Dysprosium Oxide in Global market Professional Survey 2017 : Size, Share, Trends, Industry Growth, Opportunity, Application, Production, Segmentation, Cost Structure, Company Profile, Product Picture and Specifications during the Forecast period by 2022
The report Global Dysprosium Oxide Industry 2017 is a professional, in-depth study that includes insights extracted from complex information, which clients can use for their business advantage. A large volume of precise, reliable market data has…
Global Europium Oxide Market 2017 - Longyi Heavy Rare-Earth, China Minmetals Rar …
The report studies Europium Oxide in Global market Professional Survey 2017 : Size, Share, Trends, Industry Growth, Opportunity, Application, Production, Segmentation, Cost Structure, Company Profile, Product Picture and Specifications during the Forecast period by 2022
The research report titled Europium Oxide has adopted an analytical approach to evaluate the dynamics of the Europium Oxide market. It provides a detailed analysis comprising an in-depth research on the Europium Oxide market growth drivers,…
Global Rare Earth Metals Market 2017 - Beifang Rare Earth, Xiamen Tungsten, Sunl …
Rare Earth Metals Market 2017 Industry research report provides important information to identify and analyze the market need, market size and competition. This market research report used in maintaining competitiveness over competitors.
Scope of the Report:
This report focuses on the Rare Earth Metals in Global market, especially in North America, Europe and Asia-Pacific, South America, Middle East and Africa. This report categorizes the market based on manufacturers, regions, type and application.…
