Press release
Hereditary Hematological Disorders Drug Development Pipeline Review 2018 - Acceleron Pharma, Agios Pharmaceuticals, Amarna Therapeutics, Angiocrine Bioscience, Annexin Pharmaceuticals, ArQule, Bayer
Hereditary Hematological Disorders Drug Development Pipeline Review, 2018Summary
This report provides an overview of the pipeline landscape for hereditary hematological disorders. It provides comprehensive information on the therapeutics under development and key players involved in therapeutic development for thalassemia, hemophilia B and sickle cell anemia, and features dormant and discontinued products.
Thalassemia refers to a group of inherited blood disorders that affect the body's ability to produce hemoglobin and red blood cells. Symptoms include paleness, frequent infections and jaundice. Predisposing factors include family history. Treatment includes blood transfusions and bone marrow transplant. There are 40 products in development for this indication.
FREE| Download Sample Copy at https://www.premiummarketinsights.com/sample/GBI00004572?source=OpenPR-HM
Hemophilia B is a hereditary bleeding disorder caused by a lack of blood clotting factor IX. Symptoms include bleeding into joints and associated pain and swelling, bruising, nosebleeds and prolonged bleeding from injuries and surgery. Treatment includes replacing the defective clotting factor. There are 42 products in development for this indication.
Sickle cell anemia is a genetic blood disorder in which red blood cells, which carry oxygen around the body, develop abnormally. Signs and symptoms include anemia, delayed growth, vision problems, pain and frequent infections. Treatment includes antibiotics, pain relievers, blood transfusion and stem cell transplant. There are 68 products in development for this indication.
Molecular targets acted on by products in development for hereditary hematological disorders include coagulation factors, histone deacetylases and protein kinases. Companies operating in this pipeline space include Sangamo Therapeutics, Gamida Cell and Bluebird Bio.
Scope
-Which companies are the most active within each pipeline-
-Which pharmaceutical approaches are the most prominent at each stage of the pipeline and within each indication-
-To what extent do universities and institutions play a role within this pipeline, compared to pharmaceutical companies-
-What are the most important R&D milestones and data publications to have happened in this disease area-
Reasons to buy
-Understand the overall pipeline, with an at-a-glance overview of all products in therapeutic development for each indication
-Assess the products in development in granular detail, with an up-to-date overview of each individual pipeline program in each indication and a comprehensive picture of recent updates and milestones for each
-Analyze the companies, institutions and universities currently operating in the pipeline and the products being fielded by each of these
-Understand the composition of the pipeline in terms of molecule type, molecular target, mechanism of action and route of administration
Get Discount on Report at https://www.premiummarketinsights.com/discount/GBI00004572?source=OpenPR-HM
Table of Contents:
1 Table of Contents 4
1.1 List of Tables 5
1.2 List of Figures 7
2 Introduction 8
2.1 Hereditary Hematological Disorders Report Coverage 8
2.2 Thalassemia-Overview 8
2.3 Hemophilia B-Overview 8
2.4 Sickle Cell Disease-Overview 8
3 Therapeutics Development 9
3.1 Thalassemia 9
3.2 Hemophilia B-Therapeutics Development 14
3.3 Sickle Cell Disease-Therapeutics Development 20
4 Therapeutics Assessment 28
4.1 Thalassemia-Therapeutics Assessment 28
4.2 Hemophilia B-Therapeutics Assessment 36
4.3 Sickle Cell Disease-Therapeutics Assessment 42
5 Companies Involved in Therapeutics Development 49
5.1 Thalassemia-Companies Involved in Therapeutics Development 49
5.2 Hemophilia B-Companies Involved in Therapeutics Development 59
5.3 Sickle Cell Disease-Companies Involved in Therapeutics Development 72
6 Dormant Projects 93
6.1 Thalassemia-Dormant Projects 93
6.2 Hemophilia B-Dormant Projects 94
6.3 Sickle Cell Disease-Dormant Projects 95
7 Discontinued Products 98
7.1 Thalassemia-Discontinued Products 98
7.2 Hemophilia B-Discontinued Products 98
8 Product Development Milestones 99
8.1 Thalassemia-Product Development Milestones 99
8.2 Hemophilia B-Product Development Milestones 114
8.3 Sickle Cell Disease-Product Development Milestones 127
9 Appendix 142
9.1 Methodology 142
9.2 Coverage 142
9.3 Secondary Research 142
9.4 Primary Research 142
9.5 Expert Panel Validation 142
9.6 Contact Us 143
9.7 Disclaimer 143
Premium Market Insights is a one stop shop of market research reports and solutions to various companies across the globe. We help our clients in their decision support system by helping them choose most relevant and cost effective research reports and solutions from various publishers. The market research industry has changed in last decade. As corporate focus has shifted to niche markets and emerging countries, a number of publishers have stepped in to fulfil these information needs. We have experienced and trained staff that helps you navigate different options and lets you choose best research solution at most effective cost.
Pune, India
This release was published on openPR.
Permanent link to this press release:
Copy
Please set a link in the press area of your homepage to this press release on openPR. openPR disclaims liability for any content contained in this release.
You can edit or delete your press release Hereditary Hematological Disorders Drug Development Pipeline Review 2018 - Acceleron Pharma, Agios Pharmaceuticals, Amarna Therapeutics, Angiocrine Bioscience, Annexin Pharmaceuticals, ArQule, Bayer here
News-ID: 1751288 • Views: β¦
More Releases from Premium Market Insights
The Future of HVAC: Trends and Innovations
The Europe HVAC System Market HVAC system market was valued at US$ 50,772.07 million in 2022 and is expected to reach US$ 1,25,024.86 million by 2030; it is estimated to grow at a CAGR of 11.9% from 2022 to 2030.
ππ«ππ πππ
ππ¨ ππ§π¨π° ππ¨π«πβ https://www.businessmarketinsights.com/sample/BMIRE00026922?utm_source=OpenPR&utm_medium=10694
Rise in Demand for Energy-Efficient Solutions Fuel the Europe HVAC System Market
Greenhouse gases are the primary sources of global warming and climate change. These gases absorbβ¦
Automated External Defibrillators Market New Business Opportunities and Investme β¦
The Automated External Defibrillators Market is estimated to reach US$ 2,207.94 million in 2030 from US$ 1,556.21 million by 2030; the market is projected to record a CAGR of 4.5% from 2022 to 2030.
Some of the key driving factors for the automated external defibrillators market growth are the increasing prevalence of cardiovascular diseases and rising training and awareness programs on automated external defibrillators. However, performance issues related to automated externalβ¦
Hydrolyzed Collagen Market Types and Applications, Industry Drivers, Future Dema β¦
The Hydrolyzed Collagen Market was valued at US$ 946.43 million in 2022 and is projected to reach US$ 1,322.60 million by 2028; it is expected to register a CAGR of 5.7% from 2022 to 2028.
Various end-use industries are adopting business expansion strategies and scaling production capacity to provide better customer satisfaction. For instance, in July 2020, Rousselot and Giusto Faravelli announced a distribution partnership in Italy, effective from October 2020.β¦
Aroma Ingredients Market Expectations & Growth, Trends Highlighted Until 2028
The Aroma Ingredients Market was valued at US$ 5376.90 million in 2021 and is projected to reach US$ 7692.62 million by 2028; it is expected to grow at a CAGR of 5.2% from 2021 to 2028.
Aroma ingredients are basically isolates of naturally sourced ingredients or chemically produced and are used as ingredients to add aromas or fragrance to various cosmetic and personal care products.
Based on product type, the global aromaβ¦
More Releases for Therapeutics
Adrenomyeloneuropathy Market: Epidemiology, Therapies, Companies, DelveInsight | β¦
Adrenomyeloneuropathy emerging therapies are expected to boost the Adrenomyeloneuropathy Market in the upcoming years.
DelveInsight has launched a new report on "Adrenomyeloneuropathy - Market Insights, Epidemiology, and Market Forecast-2034" that delivers an in-depth understanding of the Adrenomyeloneuropathy, historical and forecasted epidemiology as well as the Adrenomyeloneuropathy market trends in the United States, EU5 (Germany, Spain, Italy, France, and United Kingdom) and Japan.
Discover about the Adrenomyeloneuropathy market report @ https://www.delveinsight.com/report-store/adrenomyeloneuropathy-market?utm_source=openpr&utm_medium=pressrelease&utm_campaign=kpr
Some of theβ¦
Pompe Disease Market: Epidemiology, Therapies, Companies, DelveInsight | Genzyme β¦
Pompe Disease emerging therapies, such as MYOZYME (alglucosidase alfa), LUMIZYME, AAV2/8-LSPhGAA, Avalglucosidase alfa, and others, are expected to boost the Pompe Disease Market in the upcoming years.
DelveInsight has launched a new report on "Pompe Disease - Market Insights, Epidemiology, and Market Forecast-2034" that delivers an in-depth understanding of the Pompe Disease, historical and forecasted epidemiology as well as the Pompe Disease market trends in the United States, EU5 (Germany, Spain,β¦
Dark Genome Therapeutics Market Deep Research Report with Forecast to 2032 | myN β¦
The qualitative latest Research report (2025-2032) on the Dark Genome Therapeutics Market by Coherent Market Insights Provides a deep dive into key market trends, drivers, challenges, and the competitive landscape. It analyzes market size, revenue, production, and CAGR using validated methodologies to ensure precision. The report highlights tech innovation, pricing trends, consumer behavior, and investment potential - empowering businesses to make informed, strategic moves.
Request a Sample Copy: https://www.coherentmarketresearch.com/samplepages/133611
Focused on growthβ¦
Hodgkin's lymphoma Therapeutics Market Size Report 2032 | Affimed Therapeutics, β¦
DelveInsight's "Hodgkin's Lymphoma Market Insights, Epidemiology, and Market Forecast - 2032" report delivers an in-depth understanding of the Hodgkin's Lymphoma, historical and forecasted epidemiology as well as the Hodgkin's Lymphoma market trends in the United States, EU4 (Germany, Spain, Italy, and France) and the United kingdom and Japan.
Discover Key Insights into the Hodgkin's lymphoma Market with DelveInsight's In-Depth Report @ Hodgkin's lymphoma Market Size- https://www.delveinsight.com/sample-request/hodgkins-lymphoma-hl-market?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr
Key Takeaways from the Hodgkin'sβ¦
CRISPR Therapies Pipeline 2024 | Intellia Therapeutics, CRISPR therapeutics, Rep β¦
DelveInsight's, "CRISPR Therapies Pipeline Insight 2024" report provides comprehensive insights about 25+ CRISPR Therapies Companies and 30+ pipeline drugs in CRISPR Therapies pipeline landscape. It covers the CRISPR Therapies pipeline drug profiles, including clinical and nonclinical stage products. It also covers the CRISPR Therapies therapeutics assessment by product type, stage, route of administration, and molecule type. It further highlights the inactive CRISPR Therapies pipeline products in this space.
Key Takeaways fromβ¦
Digital Therapeutics Market, Digital Therapeutics Market Size, Digital Therapeut β¦
The global digital therapeutics market is expected to reach US$ 8,941.1 Mn by 2025 from US$ 1,993.2 Mn in 2017. The market is estimated to grow with a CAGR of 20.8% during the forecast period from 2018 to 2025.
North America is the largest geographic market and it is expected to be the largest revenue generator during the forecast period, whereas the market is expected to witness growth at a significantβ¦