Mucopolysaccharidosis I (MPS I) (Hurler Syndrome) Therapeutics - Pipeline Analysis 2018 | Sangamo Therapeutics, Inc., CRISPR Therapeutics

Mucopolysaccharidosis type I (MPS I) is a condition that affects many parts of the body. Earlier, MPS I disorder was divided into three separate syndromes; Hurler syndrome (MPS I-H), Hurler-Scheie syndrome (MPS I-H/S), and Scheie syndrome (MPS I-S), listed from most to least severe.

Download the sample report at: https://www.pharmaproff.com/request-sample/1144

Later on, these were clubbed as one disease, due to overlap between each of these three syndromes. Children with MPS I often have no signs or symptoms of the condition at birth, although some may have a soft out-pouching around the belly-button (umbilical hernia) or lower abdomen (inguinal hernia).

Get the detailed analysis: https://www.pharmaproff.com/report/mps-itherapeutics-pipeline-analysis

People with severe MPS I generally begin to show other signs and symptoms of the disorder within the first year of life, while those with the attenuated form have milder symptoms that develop later in childhood. Common symptoms include, large head (macrocephaly), build-up of fluid in brain (hydrocephalus), heart valve abnormalities, distinctive-looking facial features, an enlarged liver and spleen (hepatosplenomegaly), and a large tongue (macroglossia).

Make enquiry before purchase: https://www.pharmaproff.com/enquiry/1144

The drug candidates of MPS I pipeline include, but are not limited to, JOT102, SB-318 and CRISPR/Cas9. Some of the companies having drugs in the MPS I pipeline are Jupiter Orphan Therapeutics Inc., Sangamo Therapeutics Inc., and CRISPR Therapeutics Ltd.

• The report provides a comprehensive understanding of the pipeline activities covering all drug candidates under various stages of development, with the detailed analysis of pipeline and clinical trials.
• Pipeline analysis of drugs by phases includes product description and development activities including information about clinical results, designations, collaborations, licensing, grants, technology, and others.

About Us:
Pharma Proff, is a frontline market intelligence and consulting solutions provider catering to the information and data needs of burgeoning sectors across the world, including pharmaceutical and healthcare. With meticulously curated research reports on the industry landscape, we empower companies in the healthcare and pharmaceutical sectors to make informed business decisions and base their marketing strategies with astuteness.

Contact:
Pharma Proff
Toll-free: +1-888-778-7886 (USA/Canada)
International: +1-347-960-6455
Email: enquiry@pharmaproff.com
Web: https://www.pharmaproff.com

This release was published on openPR.